JP7132934B2 - ポリプロイド性アデノ随伴ウイルスベクターならびにその作製および使用の方法 - Google Patents

ポリプロイド性アデノ随伴ウイルスベクターならびにその作製および使用の方法 Download PDF

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JP7132934B2
JP7132934B2 JP2019545960A JP2019545960A JP7132934B2 JP 7132934 B2 JP7132934 B2 JP 7132934B2 JP 2019545960 A JP2019545960 A JP 2019545960A JP 2019545960 A JP2019545960 A JP 2019545960A JP 7132934 B2 JP7132934 B2 JP 7132934B2
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aav
capsid
transduction
aav8
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リチャード ジュード サムルスキ
チェンウェン リ
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University of North Carolina at Chapel Hill
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JP2019545960A 2017-03-15 2018-03-15 ポリプロイド性アデノ随伴ウイルスベクターならびにその作製および使用の方法 Active JP7132934B2 (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762471762P 2017-03-15 2017-03-15
US62/471,762 2017-03-15
US201762520901P 2017-06-16 2017-06-16
US62/520,901 2017-06-16
US201862630558P 2018-02-14 2018-02-14
US62/630,558 2018-02-14
PCT/US2018/022725 WO2018170310A1 (en) 2017-03-15 2018-03-15 Polyploid adeno-associated virus vectors and methods of making and using the same

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JP2020511127A JP2020511127A (ja) 2020-04-16
JP2020511127A5 JP2020511127A5 (https=) 2021-04-30
JP7132934B2 true JP7132934B2 (ja) 2022-09-07

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EP (3) EP3610023B1 (https=)
JP (1) JP7132934B2 (https=)
CN (2) CN110770346B (https=)
AU (2) AU2018234695B2 (https=)
CA (1) CA3054711A1 (https=)
ES (1) ES2966692T3 (https=)
IL (3) IL316259A (https=)
NZ (1) NZ756587A (https=)
WO (1) WO2018170310A1 (https=)

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CN111349148A (zh) * 2020-03-13 2020-06-30 辉大(上海)生物科技有限公司 一种腺相关病毒载体及其用途
AR122013A1 (es) * 2020-05-05 2022-08-03 Univ Duke Composiciones de virus adenoasociados compatibles entre especies y métodos para su uso
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JP2012521750A (ja) 2009-03-27 2012-09-20 プロイェクト、デ、ビオメディシナ、シーマ、ソシエダッド、リミターダ 肝硬変及び肝線維症の治療のための方法及び組成物
WO2012112578A2 (en) 2011-02-14 2012-08-23 The Children's Hospital Of Philadelphia Improved aav8 vector with enhanced functional activity and methods of use thereof
JP2015517301A (ja) 2012-05-04 2015-06-22 ノバルティス アーゲー 網膜形成不全を治療するためのウイルスベクター

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