JP7073264B2 - 遺伝子構築物 - Google Patents

遺伝子構築物 Download PDF

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JP7073264B2
JP7073264B2 JP2018540229A JP2018540229A JP7073264B2 JP 7073264 B2 JP7073264 B2 JP 7073264B2 JP 2018540229 A JP2018540229 A JP 2018540229A JP 2018540229 A JP2018540229 A JP 2018540229A JP 7073264 B2 JP7073264 B2 JP 7073264B2
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recombinant vector
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variant
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JP2018535696A5 (enExample
JP2018535696A (ja
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ウィドーソン，ピーター
マーティン，キース
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Quethera Ltd
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JP2018540229A 2015-10-26 2016-10-25 遺伝子構築物 Active JP7073264B2 (ja)

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JP2022078299A JP7503590B2 (ja) 2015-10-26 2022-05-11 遺伝子構築物

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GB1518911.1A GB2547179A (en) 2015-10-26 2015-10-26 Genetic construct
GB1518911.1 2015-10-26
PCT/GB2016/053319 WO2017072498A1 (en) 2015-10-26 2016-10-25 Genetic construct

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EP3355938B1 (en) 2015-10-01 2024-02-07 Goleini Inc. Targeted expression of chloride channels and methods of use thereof
GB201705484D0 (en) * 2017-04-05 2017-05-17 Quethera Ltd Genetic construct
US20200263196A1 (en) * 2017-09-27 2020-08-20 Sigilon Therapeutics, Inc. Methods, compositions, and implantable elements comprising active cells
EP3697916A4 (en) 2017-10-20 2021-08-11 Research Institute at Nationwide Children's Hospital METHODS AND MATERIALS FOR NT-3 GENE THERAPY
US20200399656A1 (en) * 2017-12-05 2020-12-24 University Of Washington Compositions and methods for enhancing functional expression of therapeutic genes in photoreceptors
CN108250288A (zh) * 2018-01-17 2018-07-06 吉林省农业科学院 一种叶绿体表达的脑源性神经营养因子hBDNFb蛋白及其制备方法
CN109022487A (zh) * 2018-08-15 2018-12-18 上海市第人民医院 一种表达p65的基因载体及其用于治疗视网膜神经节细胞变性的基因治疗药物
EP3863605A4 (en) * 2018-10-11 2022-10-26 Decibel Therapeutics, Inc. AAV1 VECTORS AND THEIR USES IN TREATMENT OF OTIC INDICATIONS
KR20210105382A (ko) * 2018-12-19 2021-08-26 베르사멥 아게 단백질을 코딩하는 rna
WO2020179844A1 (ja) * 2019-03-04 2020-09-10 公益財団法人東京都医学総合研究所 Ｔｒｋ断片をコードする核酸構築物、及びその利用
AU2020231228A1 (en) * 2019-03-06 2021-09-02 Generation Bio Co. Closed-ended DNA (ceDNA) and immune modulating compounds
AU2020248101A1 (en) * 2019-03-27 2021-09-16 Sigilon Therapeutics, Inc. Compositions, devices and methods for factor VII therapy
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