CN108350467B - 基因构建体 - Google Patents

基因构建体 Download PDF

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CN108350467B
CN108350467B CN201680062516.6A CN201680062516A CN108350467B CN 108350467 B CN108350467 B CN 108350467B CN 201680062516 A CN201680062516 A CN 201680062516A CN 108350467 B CN108350467 B CN 108350467B
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sequence
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recombinant vector
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CN108350467A (zh
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彼得·威多森
基思·马丁
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Quethera Ltd
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Quethera Ltd
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CN201680062516.6A 2015-10-26 2016-10-25 基因构建体 Active CN108350467B (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
GB1518911.1A GB2547179A (en) 2015-10-26 2015-10-26 Genetic construct
GB1518911.1 2015-10-26
PCT/GB2016/053319 WO2017072498A1 (en) 2015-10-26 2016-10-25 Genetic construct

Publications (2)

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CN108350467A CN108350467A (zh) 2018-07-31
CN108350467B true CN108350467B (zh) 2022-06-03

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EP (2) EP3368678B1 (enExample)
JP (2) JP7073264B2 (enExample)
KR (1) KR102819739B1 (enExample)
CN (1) CN108350467B (enExample)
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EP3697916A4 (en) 2017-10-20 2021-08-11 Research Institute at Nationwide Children's Hospital METHODS AND MATERIALS FOR NT-3 GENE THERAPY
US20200399656A1 (en) * 2017-12-05 2020-12-24 University Of Washington Compositions and methods for enhancing functional expression of therapeutic genes in photoreceptors
CN108250288A (zh) * 2018-01-17 2018-07-06 吉林省农业科学院 一种叶绿体表达的脑源性神经营养因子hBDNFb蛋白及其制备方法
CN109022487A (zh) * 2018-08-15 2018-12-18 上海市第人民医院 一种表达p65的基因载体及其用于治疗视网膜神经节细胞变性的基因治疗药物
EP3863605A4 (en) * 2018-10-11 2022-10-26 Decibel Therapeutics, Inc. AAV1 VECTORS AND THEIR USES IN TREATMENT OF OTIC INDICATIONS
KR20210105382A (ko) * 2018-12-19 2021-08-26 베르사멥 아게 단백질을 코딩하는 rna
WO2020179844A1 (ja) * 2019-03-04 2020-09-10 公益財団法人東京都医学総合研究所 Ｔｒｋ断片をコードする核酸構築物、及びその利用
AU2020231228A1 (en) * 2019-03-06 2021-09-02 Generation Bio Co. Closed-ended DNA (ceDNA) and immune modulating compounds
AU2020248101A1 (en) * 2019-03-27 2021-09-16 Sigilon Therapeutics, Inc. Compositions, devices and methods for factor VII therapy
JP2022536692A (ja) 2019-06-11 2022-08-18 シャイアー ヒューマン ジェネティック セラピーズ インコーポレイテッド 調節不全の血漿カリクレインによって媒介される疾患の治療のための抗体のアデノ随伴ウイルスベクター送達
AU2020314866A1 (en) * 2019-07-18 2022-02-03 Lysogene Compositions and methods for the treatment of Sanfilippo disease and other disorders
RU2719013C1 (ru) * 2019-09-25 2020-04-16 Федеральное государственное бюджетное образовательное учреждение высшего образования "Московский государственный университет имени М.В. Ломоносова" (МГУ) Генно-инженерная конструкция для стимуляции посттравматической регенерации периферических нервов
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