JP6174678B2 - 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド - Google Patents

神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド Download PDF

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JP6174678B2
JP6174678B2 JP2015506930A JP2015506930A JP6174678B2 JP 6174678 B2 JP6174678 B2 JP 6174678B2 JP 2015506930 A JP2015506930 A JP 2015506930A JP 2015506930 A JP2015506930 A JP 2015506930A JP 6174678 B2 JP6174678 B2 JP 6174678B2
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JP2015514418A5 (enExample
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ヴィッサー， ピーター クリスチャン デ
ヴィッサー， ピーター クリスチャン デ
スーザン アレゴンダ マリア マルダーズ，
スーザン アレゴンダ マリア マルダーズ，
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バイオマリン テクノロジーズ ベー．フェー．
バイオマリン テクノロジーズ ベー．フェー．
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JP2015506930A 2012-04-23 2013-04-23 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド Active JP6174678B2 (ja)

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US201261636914P 2012-04-23 2012-04-23
EP12165139.2 2012-04-23
US61/636,914 2012-04-23
EP12165139 2012-04-23
PCT/NL2013/050306 WO2013162363A1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders

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JP2017133005A Pending JP2018027080A (ja) 2012-04-23 2017-07-06 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド
JP2020115868A Active JP7459691B2 (ja) 2012-04-23 2020-07-03 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド
JP2022093254A Pending JP2022126711A (ja) 2012-04-23 2022-06-08 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド
JP2025061303A Pending JP2025111478A (ja) 2012-04-23 2025-04-02 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド

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JP2020115868A Active JP7459691B2 (ja) 2012-04-23 2020-07-03 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド
JP2022093254A Pending JP2022126711A (ja) 2012-04-23 2022-06-08 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド
JP2025061303A Pending JP2025111478A (ja) 2012-04-23 2025-04-02 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド

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JP2020182472A (ja) * 2012-04-23 2020-11-12 バイオマリン テクノロジーズ ベー．フェー． 神経筋障害の治療のための改善された特徴を有するｒｎａ調節オリゴヌクレオチド

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