HRP20171254T1 - Oligonukleotidi koji moduliraju rnk s poboljšanim karakteristikama za liječenje neuromišićnih poremećaja - Google Patents

Oligonukleotidi koji moduliraju rnk s poboljšanim karakteristikama za liječenje neuromišićnih poremećaja

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Publication number
HRP20171254T1
HRP20171254T1 HRP20171254TT HRP20171254T HRP20171254T1 HR P20171254 T1 HRP20171254 T1 HR P20171254T1 HR P20171254T T HRP20171254T T HR P20171254TT HR P20171254 T HRP20171254 T HR P20171254T HR P20171254 T1 HRP20171254 T1 HR P20171254T1
Authority
HR
Croatia
Prior art keywords
rna
treatment
neuromuscular disorders
enhanced characteristics
modulating oligonucleotides
Prior art date
Application number
HRP20171254TT
Other languages
English (en)
Croatian (hr)
Inventor
Peter Christian De Visser
Susan Allegonda Maria MULDERS
Original Assignee
Biomarin Technologies B.V.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Biomarin Technologies B.V. filed Critical Biomarin Technologies B.V.
Publication of HRP20171254T1 publication Critical patent/HRP20171254T1/hr

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    • C12N15/09—Recombinant DNA-technology
    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A—HUMAN NECESSITIES
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    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A61P21/02—Muscle relaxants, e.g. for tetanus or cramps
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HRP20171254TT 2012-04-23 2013-04-23 Oligonukleotidi koji moduliraju rnk s poboljšanim karakteristikama za liječenje neuromišićnih poremećaja HRP20171254T1 (hr)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201261636914P 2012-04-23 2012-04-23
EP12165139 2012-04-23
EP13720617.3A EP2841578B1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders
PCT/NL2013/050306 WO2013162363A1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders

Publications (1)

Publication Number Publication Date
HRP20171254T1 true HRP20171254T1 (hr) 2018-01-12

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HRP20171254TT HRP20171254T1 (hr) 2012-04-23 2013-04-23 Oligonukleotidi koji moduliraju rnk s poboljšanim karakteristikama za liječenje neuromišićnih poremećaja

Country Status (19)

Country Link
US (5) US9745576B2 (enExample)
EP (4) EP2841578B1 (enExample)
JP (5) JP6174678B2 (enExample)
CN (2) CN110025628B (enExample)
AU (1) AU2013253074C1 (enExample)
BR (1) BR112014026285B1 (enExample)
CA (2) CA2870697C (enExample)
DK (1) DK2841578T3 (enExample)
ES (2) ES2983421T3 (enExample)
HR (1) HRP20171254T1 (enExample)
HU (1) HUE033431T2 (enExample)
LT (1) LT2841578T (enExample)
NZ (1) NZ700561A (enExample)
PL (2) PL3604536T3 (enExample)
PT (1) PT2841578T (enExample)
RS (1) RS56319B1 (enExample)
SI (1) SI2841578T1 (enExample)
SM (1) SMT201700339T1 (enExample)
WO (1) WO2013162363A1 (enExample)

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