CN104271741A - 用于治疗神经肌肉障碍的具有改善特性的rna调节寡核苷酸 - Google Patents

用于治疗神经肌肉障碍的具有改善特性的rna调节寡核苷酸 Download PDF

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CN104271741A
CN104271741A CN201380021505.XA CN201380021505A CN104271741A CN 104271741 A CN104271741 A CN 104271741A CN 201380021505 A CN201380021505 A CN 201380021505A CN 104271741 A CN104271741 A CN 104271741A
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oligonucleotide
nucleotides
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彼得·克里斯蒂安·德菲瑟
苏珊·阿列贡达·玛丽亚·马尔德斯
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PROSENSA TECHNOLOGIES BV
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CN201380021505.XA 2012-04-23 2013-04-23 用于治疗神经肌肉障碍的具有改善特性的rna调节寡核苷酸 Pending CN104271741A (zh)

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US201261636914P 2012-04-23 2012-04-23
EP12165139.2 2012-04-23
US61/636,914 2012-04-23
EP12165139 2012-04-23
PCT/NL2013/050306 WO2013162363A1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders

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