SMT201700339T1 - Oligonucleotidi di modulazione dell'rna con caratteristiche migliorate per il trattamento dei disturbi neuromuscolari - Google Patents

Oligonucleotidi di modulazione dell'rna con caratteristiche migliorate per il trattamento dei disturbi neuromuscolari

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Publication number
SMT201700339T1
SMT201700339T1 SM20170339T SMT201700339T SMT201700339T1 SM T201700339 T1 SMT201700339 T1 SM T201700339T1 SM 20170339 T SM20170339 T SM 20170339T SM T201700339 T SMT201700339 T SM T201700339T SM T201700339 T1 SMT201700339 T1 SM T201700339T1
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San Marino
Prior art keywords
treatment
improved characteristics
neuromuscular disorders
modulating oligonucleotides
rna modulating
Prior art date
Application number
SM20170339T
Other languages
English (en)
Italian (it)
Inventor
Visser Peter Christian De
Susan Allegonda Maria Mulders
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Biomarin Tech Bv
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Filing date
Publication date
Application filed by Biomarin Tech Bv filed Critical Biomarin Tech Bv
Publication of SMT201700339T1 publication Critical patent/SMT201700339T1/it

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    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
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    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A61P21/02—Muscle relaxants, e.g. for tetanus or cramps
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SM20170339T 2012-04-23 2013-04-23 Oligonucleotidi di modulazione dell'rna con caratteristiche migliorate per il trattamento dei disturbi neuromuscolari SMT201700339T1 (it)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201261636914P 2012-04-23 2012-04-23
EP12165139 2012-04-23
EP13720617.3A EP2841578B1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders
PCT/NL2013/050306 WO2013162363A1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders

Publications (1)

Publication Number Publication Date
SMT201700339T1 true SMT201700339T1 (it) 2017-09-07

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SM20170339T SMT201700339T1 (it) 2012-04-23 2013-04-23 Oligonucleotidi di modulazione dell'rna con caratteristiche migliorate per il trattamento dei disturbi neuromuscolari

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Country Link
US (5) US9745576B2 (enExample)
EP (4) EP3604536B1 (enExample)
JP (5) JP6174678B2 (enExample)
CN (2) CN104271741A (enExample)
AU (1) AU2013253074C1 (enExample)
BR (1) BR112014026285B1 (enExample)
CA (2) CA3103101C (enExample)
DK (1) DK2841578T3 (enExample)
ES (2) ES2639066T3 (enExample)
HR (1) HRP20171254T1 (enExample)
HU (1) HUE033431T2 (enExample)
LT (1) LT2841578T (enExample)
NZ (1) NZ700561A (enExample)
PL (2) PL2841578T3 (enExample)
PT (1) PT2841578T (enExample)
RS (1) RS56319B1 (enExample)
SI (1) SI2841578T1 (enExample)
SM (1) SMT201700339T1 (enExample)
WO (1) WO2013162363A1 (enExample)

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US20220389421A1 (en) 2022-12-08
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