JP2024537797A5 - - Google Patents

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Publication number
JP2024537797A5
JP2024537797A5 JP2024519554A JP2024519554A JP2024537797A5 JP 2024537797 A5 JP2024537797 A5 JP 2024537797A5 JP 2024519554 A JP2024519554 A JP 2024519554A JP 2024519554 A JP2024519554 A JP 2024519554A JP 2024537797 A5 JP2024537797 A5 JP 2024537797A5
Authority
JP
Japan
Prior art keywords
sequence
nucleic acid
acid molecule
nucleotide sequence
seq
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024519554A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024537797A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/077228 external-priority patent/WO2023056331A1/en
Publication of JP2024537797A publication Critical patent/JP2024537797A/ja
Publication of JP2024537797A5 publication Critical patent/JP2024537797A5/ja
Pending legal-status Critical Current

Links

JP2024519554A 2021-09-30 2022-09-29 低下した免疫原性を有する第viii因子ポリペプチドをコードする核酸 Pending JP2024537797A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163250575P 2021-09-30 2021-09-30
US63/250,575 2021-09-30
PCT/US2022/077228 WO2023056331A1 (en) 2021-09-30 2022-09-29 Nucleic acids encoding factor viii polypeptides with reduced immunogenicity

Publications (2)

Publication Number Publication Date
JP2024537797A JP2024537797A (ja) 2024-10-16
JP2024537797A5 true JP2024537797A5 (enExample) 2025-10-06

Family

ID=83996337

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024519554A Pending JP2024537797A (ja) 2021-09-30 2022-09-29 低下した免疫原性を有する第viii因子ポリペプチドをコードする核酸

Country Status (11)

Country Link
US (1) US20240350672A1 (enExample)
EP (1) EP4408874A1 (enExample)
JP (1) JP2024537797A (enExample)
KR (1) KR20240067122A (enExample)
CN (1) CN118019758A (enExample)
AU (1) AU2022355088A1 (enExample)
CA (1) CA3232988A1 (enExample)
IL (1) IL311725A (enExample)
MX (1) MX2024003963A (enExample)
TW (1) TW202346327A (enExample)
WO (1) WO2023056331A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
RS61387B2 (sr) 2013-02-15 2024-06-28 Bioverativ Therapeutics Inc Gen optimizovanog faktora viii

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ATE87663T1 (de) 1986-01-03 1993-04-15 Genetics Inst Verfahren zur herstellung von faktor-viii:c-typ- proteinen.
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CN111548418A (zh) * 2012-02-15 2020-08-18 比奥贝拉蒂治疗公司 因子viii组合物及其制备和使用方法
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JP7602454B2 (ja) * 2018-08-09 2024-12-18 バイオベラティブ セラピューティクス インコーポレイテッド 核酸分子及び非ウイルス遺伝子治療のためのそれらの使用
JP7803014B2 (ja) * 2019-09-30 2026-01-21 バイオベラティブ セラピューティクス インコーポレイテッド レンチウイルスベクター製剤

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