JP2024534415A5 - - Google Patents
Info
- Publication number
- JP2024534415A5 JP2024534415A5 JP2024516751A JP2024516751A JP2024534415A5 JP 2024534415 A5 JP2024534415 A5 JP 2024534415A5 JP 2024516751 A JP2024516751 A JP 2024516751A JP 2024516751 A JP2024516751 A JP 2024516751A JP 2024534415 A5 JP2024534415 A5 JP 2024534415A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- vector
- promoter
- itr2
- itr1
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163245666P | 2021-09-17 | 2021-09-17 | |
| US63/245,666 | 2021-09-17 | ||
| US202263331441P | 2022-04-15 | 2022-04-15 | |
| US63/331,441 | 2022-04-15 | ||
| US202263341737P | 2022-05-13 | 2022-05-13 | |
| US63/341,737 | 2022-05-13 | ||
| PCT/US2022/076563 WO2023044424A1 (en) | 2021-09-17 | 2022-09-16 | Frataxin gene therapy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024534415A JP2024534415A (ja) | 2024-09-20 |
| JP2024534415A5 true JP2024534415A5 (https=) | 2025-09-24 |
Family
ID=85603625
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024516751A Pending JP2024534415A (ja) | 2021-09-17 | 2022-09-16 | フラタキシン遺伝子療法 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20240376497A1 (https=) |
| EP (1) | EP4401756A4 (https=) |
| JP (1) | JP2024534415A (https=) |
| KR (1) | KR20240082353A (https=) |
| AU (1) | AU2022345283A1 (https=) |
| CA (1) | CA3231881A1 (https=) |
| CO (1) | CO2024004573A2 (https=) |
| IL (1) | IL311499A (https=) |
| MX (1) | MX2024003241A (https=) |
| TW (1) | TW202321455A (https=) |
| WO (1) | WO2023044424A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2018089527A1 (en) | 2016-11-09 | 2018-05-17 | Intrexon Corporation | Frataxin expression constructs |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2018089527A1 (en) * | 2016-11-09 | 2018-05-17 | Intrexon Corporation | Frataxin expression constructs |
| EP4089173A1 (en) * | 2017-10-17 | 2022-11-16 | Fundació Institut d'Investigació en Ciències de la Salut Germans Trias i Pujol | Vectors for the treatment of friedreich's ataxia |
| WO2020106916A1 (en) * | 2018-11-21 | 2020-05-28 | Stridebio, Inc. | Recombinant viral vectors and nucleic acids for producing the same |
| CA3162020A1 (en) * | 2019-12-19 | 2021-06-24 | James M. Wilson | Compositions for treating friedreich's ataxia |
-
2022
- 2022-09-16 IL IL311499A patent/IL311499A/en unknown
- 2022-09-16 US US18/692,672 patent/US20240376497A1/en active Pending
- 2022-09-16 CA CA3231881A patent/CA3231881A1/en active Pending
- 2022-09-16 KR KR1020247012580A patent/KR20240082353A/ko active Pending
- 2022-09-16 MX MX2024003241A patent/MX2024003241A/es unknown
- 2022-09-16 EP EP22870975.4A patent/EP4401756A4/en active Pending
- 2022-09-16 JP JP2024516751A patent/JP2024534415A/ja active Pending
- 2022-09-16 WO PCT/US2022/076563 patent/WO2023044424A1/en not_active Ceased
- 2022-09-16 AU AU2022345283A patent/AU2022345283A1/en active Pending
- 2022-09-19 TW TW111135360A patent/TW202321455A/zh unknown
-
2024
- 2024-04-11 CO CONC2024/0004573A patent/CO2024004573A2/es unknown
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