JP2024534415A5 - - Google Patents

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Publication number
JP2024534415A5
JP2024534415A5 JP2024516751A JP2024516751A JP2024534415A5 JP 2024534415 A5 JP2024534415 A5 JP 2024534415A5 JP 2024516751 A JP2024516751 A JP 2024516751A JP 2024516751 A JP2024516751 A JP 2024516751A JP 2024534415 A5 JP2024534415 A5 JP 2024534415A5
Authority
JP
Japan
Application number
JP2024516751A
Other languages
Japanese (ja)
Other versions
JP2024534415A (ja
JPWO2023044424A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/076563 external-priority patent/WO2023044424A1/en
Publication of JP2024534415A publication Critical patent/JP2024534415A/ja
Publication of JP2024534415A5 publication Critical patent/JP2024534415A5/ja
Publication of JPWO2023044424A5 publication Critical patent/JPWO2023044424A5/ja
Pending legal-status Critical Current

Links

JP2024516751A 2021-09-17 2022-09-16 フラタキシン遺伝子療法 Pending JP2024534415A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202163245666P 2021-09-17 2021-09-17
US63/245,666 2021-09-17
US202263331441P 2022-04-15 2022-04-15
US63/331,441 2022-04-15
US202263341737P 2022-05-13 2022-05-13
US63/341,737 2022-05-13
PCT/US2022/076563 WO2023044424A1 (en) 2021-09-17 2022-09-16 Frataxin gene therapy

Publications (3)

Publication Number Publication Date
JP2024534415A JP2024534415A (ja) 2024-09-20
JP2024534415A5 true JP2024534415A5 (https=) 2025-09-24
JPWO2023044424A5 JPWO2023044424A5 (https=) 2025-09-24

Family

ID=85603625

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024516751A Pending JP2024534415A (ja) 2021-09-17 2022-09-16 フラタキシン遺伝子療法

Country Status (11)

Country Link
US (1) US20240376497A1 (https=)
EP (1) EP4401756A4 (https=)
JP (1) JP2024534415A (https=)
KR (1) KR20240082353A (https=)
AU (1) AU2022345283A1 (https=)
CA (1) CA3231881A1 (https=)
CO (1) CO2024004573A2 (https=)
IL (1) IL311499A (https=)
MX (1) MX2024003241A (https=)
TW (1) TW202321455A (https=)
WO (1) WO2023044424A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN110139933B (zh) 2016-11-09 2024-03-08 英特瑞克斯顿股份有限公司 共济蛋白表达构建体

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN110139933B (zh) * 2016-11-09 2024-03-08 英特瑞克斯顿股份有限公司 共济蛋白表达构建体
WO2019076973A1 (en) * 2017-10-17 2019-04-25 Fundació Institut D'investigació En Ciències De La Salut Germans Trias I Pujol VECTORS FOR THE TREATMENT OF FRIEDREICH ATAXIA
AU2019385506A1 (en) * 2018-11-21 2021-06-03 Takeda Pharmaceutical Company Limited Recombinant viral vectors and nucleic acids for producing the same
EP4085144A4 (en) * 2019-12-19 2024-03-27 The Trustees of The University of Pennsylvania COMPOSITIONS FOR THE TREATMENT OF FRIEDREICH AAXIA

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