JP2025508743A5 - - Google Patents
Info
- Publication number
- JP2025508743A5 JP2025508743A5 JP2024548600A JP2024548600A JP2025508743A5 JP 2025508743 A5 JP2025508743 A5 JP 2025508743A5 JP 2024548600 A JP2024548600 A JP 2024548600A JP 2024548600 A JP2024548600 A JP 2024548600A JP 2025508743 A5 JP2025508743 A5 JP 2025508743A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- nucleic acid
- subject
- therapeutically effective
- compared
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263311840P | 2022-02-18 | 2022-02-18 | |
| US63/311,840 | 2022-02-18 | ||
| US202263383639P | 2022-11-14 | 2022-11-14 | |
| US63/383,639 | 2022-11-14 | ||
| PCT/US2023/062834 WO2023159190A1 (en) | 2022-02-18 | 2023-02-17 | Gene therapy for arrhythmogenic cardiomyopathy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025508743A JP2025508743A (ja) | 2025-04-10 |
| JP2025508743A5 true JP2025508743A5 (https=) | 2026-02-26 |
Family
ID=85703556
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024548600A Pending JP2025508743A (ja) | 2022-02-18 | 2023-02-17 | 不整脈原性心筋症のための遺伝子治療 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20250144245A1 (https=) |
| EP (1) | EP4479543A1 (https=) |
| JP (1) | JP2025508743A (https=) |
| CN (1) | CN119013408A (https=) |
| AU (1) | AU2023221412A1 (https=) |
| CA (1) | CA3244528A1 (https=) |
| WO (1) | WO2023159190A1 (https=) |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20070003528A1 (en) | 2005-06-29 | 2007-01-04 | Paul Consigny | Intracoronary device and method of use thereof |
| US7774057B2 (en) | 2005-09-06 | 2010-08-10 | Cardiac Pacemakers, Inc. | Method and apparatus for device controlled gene expression for cardiac protection |
| US9138596B2 (en) | 2007-08-22 | 2015-09-22 | Cardiac Pacemakers, Inc. | Optical depolarization of cardiac tissue |
| ITTO20130669A1 (it) | 2013-08-05 | 2015-02-06 | Consiglio Nazionale Ricerche | Vettore adeno-associato ricombinante muscolo-specifico e suo impiego nel trattamento di patologie muscolari |
| ES2976559T3 (es) * | 2017-09-20 | 2024-08-05 | Univ California | Terapia génica con conexina 43 para restaurar la función eléctrica y cardíaca y la estructura cardíaca, en la miocardiopatía arritmogénica del ventrículo derecho |
| TWI897882B (zh) * | 2019-09-20 | 2025-09-21 | 英商Ucl商業有限責任公司 | 右心室心律失常性心肌病之基因療法組合物及治療 |
| KR20230042468A (ko) * | 2020-08-05 | 2023-03-28 | 스페이스크래프트 세븐, 엘엘씨 | Csrp3 (시스테인 및 글리신 풍부 단백질 3) 유전자 요법 |
-
2023
- 2023-02-17 JP JP2024548600A patent/JP2025508743A/ja active Pending
- 2023-02-17 WO PCT/US2023/062834 patent/WO2023159190A1/en not_active Ceased
- 2023-02-17 CN CN202380034073.XA patent/CN119013408A/zh active Pending
- 2023-02-17 AU AU2023221412A patent/AU2023221412A1/en active Pending
- 2023-02-17 CA CA3244528A patent/CA3244528A1/en active Pending
- 2023-02-17 EP EP23711901.1A patent/EP4479543A1/en active Pending
- 2023-02-17 US US18/838,928 patent/US20250144245A1/en active Pending
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