JP2025508743A5 - - Google Patents

Info

Publication number
JP2025508743A5
JP2025508743A5 JP2024548600A JP2024548600A JP2025508743A5 JP 2025508743 A5 JP2025508743 A5 JP 2025508743A5 JP 2024548600 A JP2024548600 A JP 2024548600A JP 2024548600 A JP2024548600 A JP 2024548600A JP 2025508743 A5 JP2025508743 A5 JP 2025508743A5
Authority
JP
Japan
Prior art keywords
aav
nucleic acid
subject
therapeutically effective
compared
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024548600A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025508743A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/062834 external-priority patent/WO2023159190A1/en
Publication of JP2025508743A publication Critical patent/JP2025508743A/ja
Publication of JP2025508743A5 publication Critical patent/JP2025508743A5/ja
Pending legal-status Critical Current

Links

JP2024548600A 2022-02-18 2023-02-17 不整脈原性心筋症のための遺伝子治療 Pending JP2025508743A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263311840P 2022-02-18 2022-02-18
US63/311,840 2022-02-18
US202263383639P 2022-11-14 2022-11-14
US63/383,639 2022-11-14
PCT/US2023/062834 WO2023159190A1 (en) 2022-02-18 2023-02-17 Gene therapy for arrhythmogenic cardiomyopathy

Publications (2)

Publication Number Publication Date
JP2025508743A JP2025508743A (ja) 2025-04-10
JP2025508743A5 true JP2025508743A5 (https=) 2026-02-26

Family

ID=85703556

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024548600A Pending JP2025508743A (ja) 2022-02-18 2023-02-17 不整脈原性心筋症のための遺伝子治療

Country Status (7)

Country Link
US (1) US20250144245A1 (https=)
EP (1) EP4479543A1 (https=)
JP (1) JP2025508743A (https=)
CN (1) CN119013408A (https=)
AU (1) AU2023221412A1 (https=)
CA (1) CA3244528A1 (https=)
WO (1) WO2023159190A1 (https=)

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20070003528A1 (en) 2005-06-29 2007-01-04 Paul Consigny Intracoronary device and method of use thereof
US7774057B2 (en) 2005-09-06 2010-08-10 Cardiac Pacemakers, Inc. Method and apparatus for device controlled gene expression for cardiac protection
US9138596B2 (en) 2007-08-22 2015-09-22 Cardiac Pacemakers, Inc. Optical depolarization of cardiac tissue
ITTO20130669A1 (it) 2013-08-05 2015-02-06 Consiglio Nazionale Ricerche Vettore adeno-associato ricombinante muscolo-specifico e suo impiego nel trattamento di patologie muscolari
ES2976559T3 (es) * 2017-09-20 2024-08-05 Univ California Terapia génica con conexina 43 para restaurar la función eléctrica y cardíaca y la estructura cardíaca, en la miocardiopatía arritmogénica del ventrículo derecho
TWI897882B (zh) * 2019-09-20 2025-09-21 英商Ucl商業有限責任公司 右心室心律失常性心肌病之基因療法組合物及治療
KR20230042468A (ko) * 2020-08-05 2023-03-28 스페이스크래프트 세븐, 엘엘씨 Csrp3 (시스테인 및 글리신 풍부 단백질 3) 유전자 요법

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