JP2024167419A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2024167419A5 JP2024167419A5 JP2024156801A JP2024156801A JP2024167419A5 JP 2024167419 A5 JP2024167419 A5 JP 2024167419A5 JP 2024156801 A JP2024156801 A JP 2024156801A JP 2024156801 A JP2024156801 A JP 2024156801A JP 2024167419 A5 JP2024167419 A5 JP 2024167419A5
- Authority
- JP
- Japan
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201662274700P | 2016-01-04 | 2016-01-04 | |
| US62/274,700 | 2016-01-04 | ||
| US201662414533P | 2016-10-28 | 2016-10-28 | |
| US62/414,533 | 2016-10-28 | ||
| JP2018534551A JP7159048B2 (ja) | 2016-01-04 | 2017-01-03 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
| PCT/US2017/012061 WO2017120147A1 (en) | 2016-01-04 | 2017-01-03 | Gene therapy for recessive dystrophic epidermolysis bullosa using genetically corrected autologous keratinocytes |
| JP2022164008A JP7555380B2 (ja) | 2016-01-04 | 2022-10-12 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022164008A Division JP7555380B2 (ja) | 2016-01-04 | 2022-10-12 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024167419A JP2024167419A (ja) | 2024-12-03 |
| JP2024167419A5 true JP2024167419A5 (enExample) | 2025-04-02 |
Family
ID=58010360
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018534551A Active JP7159048B2 (ja) | 2016-01-04 | 2017-01-03 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
| JP2022164008A Active JP7555380B2 (ja) | 2016-01-04 | 2022-10-12 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
| JP2024156801A Pending JP2024167419A (ja) | 2016-01-04 | 2024-09-10 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
Family Applications Before (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018534551A Active JP7159048B2 (ja) | 2016-01-04 | 2017-01-03 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
| JP2022164008A Active JP7555380B2 (ja) | 2016-01-04 | 2022-10-12 | 遺伝子修正自己ケラチノサイトを使用する劣性栄養障害型表皮水疱症のための遺伝子療法 |
Country Status (17)
| Country | Link |
|---|---|
| US (4) | US12173314B2 (enExample) |
| EP (2) | EP3842520A1 (enExample) |
| JP (3) | JP7159048B2 (enExample) |
| KR (1) | KR20180093967A (enExample) |
| CN (2) | CN108473952B (enExample) |
| AU (2) | AU2017205925B2 (enExample) |
| BR (1) | BR112018013576A2 (enExample) |
| CA (1) | CA3008676A1 (enExample) |
| DK (1) | DK3400287T3 (enExample) |
| ES (1) | ES2861453T3 (enExample) |
| IL (2) | IL260038B (enExample) |
| MX (1) | MX2018007986A (enExample) |
| NZ (1) | NZ743682A (enExample) |
| PT (1) | PT3400287T (enExample) |
| RU (2) | RU2753248C2 (enExample) |
| WO (1) | WO2017120147A1 (enExample) |
| ZA (1) | ZA201803962B (enExample) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN108473952B (zh) * | 2016-01-04 | 2022-04-08 | 小利兰·斯坦福大学托管委员会 | 使用经遗传矫正的自体角质形成细胞进行的隐性营养不良型大疱性表皮松解症的基因疗法 |
| IT201700094210A1 (it) * | 2017-08-17 | 2019-02-17 | Holostem Terapie Avanzate S R L | Metodo per produrre lembi cellulari |
| IT201700104587A1 (it) * | 2017-09-19 | 2019-03-19 | Holostem Terapie Avanzate S R L | Usi terapeutici di lembi di cellule geneticamente modificate |
| KR102227434B1 (ko) * | 2017-12-29 | 2021-03-16 | 진메디신 주식회사 | 유전자 전달용 세포 시트 |
| RU2730661C2 (ru) * | 2018-12-27 | 2020-08-24 | Селл энд Джин Терапи Лтд | Генотерапевтический ДНК-вектор на основе генотерапевтического ДНК-вектора VTvaf17, несущий целевой ген, выбранный из группы генов COL1A1, COL1A2, P4HA1, P4HA2, COL7A1, CLCA2, ELN, PLOD1 для повышения уровня экспрессии этих целевых генов, способ его получения и применения, штамм Escherichia coli SCS110-AF/VTvaf17-COL1A1, или Escherichia coli SCS110-AF/VTvaf17-COL1A2, или Escherichia coli SCS110-AF/VTvaf17-P4HA1, или Escherichia coli SCS110-AF/VTvaf17-P4HA2, или Escherichia coli SCS110-AF/VTvaf17-COL7A1, или Escherichia coli SCS110-AF/VTvaf17-CLCA2, или Escherichia coli SCS110-AF/VTvaf17-ELN, или Escherichia coli SCS110-AF/VTvaf17- PLOD1, несущий генотерапевтический ДНК-вектор, способ его получения, способ производства в промышленных масштабах генотерапевтического ДНК-вектора |
| AU2020209687A1 (en) | 2019-01-18 | 2021-07-29 | Osaka University | Composition for use in treating dystrophic epidermolysis bullosa |
| CN116529361B (zh) * | 2019-10-18 | 2024-01-26 | 北赛泓升(北京)生物科技有限公司 | 使用多顺反子sox2、klf4和任选的c-myc产生诱导多能干细胞 |
| AU2020459825A1 (en) * | 2020-07-22 | 2023-03-16 | Osaka University | Therapeutic agent for dystrophic epidermolysis bullosa |
| WO2023064806A1 (en) | 2021-10-12 | 2023-04-20 | Phoenix Tissue Repair, Inc. | Collagen 7 protein replacement therapy |
| JP2025094280A (ja) * | 2022-01-21 | 2025-06-25 | 国立大学法人大阪大学 | 細胞シート |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5830725A (en) * | 1995-04-28 | 1998-11-03 | The Board Of Trustees For The Leland Stanford Junior University | Rapid, stable high-titre production of recombing retrovirus |
| US20020090725A1 (en) | 2000-11-17 | 2002-07-11 | Simpson David G. | Electroprocessed collagen |
| WO2001002433A1 (en) * | 1999-07-02 | 2001-01-11 | Human Genome Sciences, Inc. | Keratinocyte growth factor-2 |
| FR2857671B1 (fr) * | 2003-07-18 | 2007-10-05 | Centre Nat Rech Scient | Nouveau procede de culture de keratinocytes et ses applications |
| CN1916166B (zh) * | 2006-09-08 | 2010-08-11 | 北京赛尔泰和生物医药科技有限公司 | 自体角膜上皮的制备方法 |
| US8865199B2 (en) * | 2008-11-17 | 2014-10-21 | Ingeneron, Inc. | Biomatrix composition and methods of biomatrix seeding |
| GB201202561D0 (en) * | 2012-02-15 | 2012-03-28 | Univ Dundee | Treatment of skin disorders |
| WO2014074503A1 (en) * | 2012-11-06 | 2014-05-15 | Imbed Biosciences, Inc. | Methods and compositions for wound healing |
| US8697359B1 (en) | 2012-12-12 | 2014-04-15 | The Broad Institute, Inc. | CRISPR-Cas systems and methods for altering expression of gene products |
| CN105087565A (zh) * | 2015-08-21 | 2015-11-25 | 内蒙古自治区人民医院 | 一种营养不良型大疱性表皮松解症核苷酸及其应用 |
| CN108473952B (zh) * | 2016-01-04 | 2022-04-08 | 小利兰·斯坦福大学托管委员会 | 使用经遗传矫正的自体角质形成细胞进行的隐性营养不良型大疱性表皮松解症的基因疗法 |
| CN109257926A (zh) * | 2016-03-18 | 2019-01-22 | 英特拉克森公司 | 用于治疗vii型胶原缺乏的组合物和方法 |
-
2017
- 2017-01-03 CN CN201780005233.2A patent/CN108473952B/zh not_active Expired - Fee Related
- 2017-01-03 EP EP20210538.3A patent/EP3842520A1/en active Pending
- 2017-01-03 BR BR112018013576A patent/BR112018013576A2/pt not_active Application Discontinuation
- 2017-01-03 JP JP2018534551A patent/JP7159048B2/ja active Active
- 2017-01-03 RU RU2018127524A patent/RU2753248C2/ru active
- 2017-01-03 EP EP17704327.0A patent/EP3400287B1/en active Active
- 2017-01-03 KR KR1020187018813A patent/KR20180093967A/ko not_active Ceased
- 2017-01-03 ES ES17704327T patent/ES2861453T3/es active Active
- 2017-01-03 CA CA3008676A patent/CA3008676A1/en active Pending
- 2017-01-03 AU AU2017205925A patent/AU2017205925B2/en not_active Ceased
- 2017-01-03 IL IL260038A patent/IL260038B/en unknown
- 2017-01-03 PT PT177043270T patent/PT3400287T/pt unknown
- 2017-01-03 DK DK17704327.0T patent/DK3400287T3/da active
- 2017-01-03 NZ NZ743682A patent/NZ743682A/en not_active IP Right Cessation
- 2017-01-03 US US16/066,253 patent/US12173314B2/en active Active
- 2017-01-03 RU RU2021121824A patent/RU2021121824A/ru unknown
- 2017-01-03 CN CN202210368934.5A patent/CN114699558B/zh not_active Expired - Fee Related
- 2017-01-03 WO PCT/US2017/012061 patent/WO2017120147A1/en not_active Ceased
- 2017-01-03 MX MX2018007986A patent/MX2018007986A/es unknown
-
2018
- 2018-06-13 ZA ZA2018/03962A patent/ZA201803962B/en unknown
-
2020
- 2020-09-25 AU AU2020239779A patent/AU2020239779A1/en not_active Abandoned
-
2022
- 2022-05-31 IL IL293465A patent/IL293465B2/en unknown
- 2022-10-12 JP JP2022164008A patent/JP7555380B2/ja active Active
-
2023
- 2023-11-03 US US18/501,837 patent/US12110504B2/en active Active
-
2024
- 2024-09-10 JP JP2024156801A patent/JP2024167419A/ja active Pending
- 2024-10-31 US US18/933,687 patent/US12385010B2/en active Active
-
2025
- 2025-04-29 US US19/192,918 patent/US20250257319A1/en active Pending