JP2023548295A5 - - Google Patents

Info

Publication number
JP2023548295A5
JP2023548295A5 JP2023525517A JP2023525517A JP2023548295A5 JP 2023548295 A5 JP2023548295 A5 JP 2023548295A5 JP 2023525517 A JP2023525517 A JP 2023525517A JP 2023525517 A JP2023525517 A JP 2023525517A JP 2023548295 A5 JP2023548295 A5 JP 2023548295A5
Authority
JP
Japan
Prior art keywords
compound
salt
formula
absent
linking group
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023525517A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023548295A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/058232 external-priority patent/WO2022098990A1/en
Publication of JP2023548295A publication Critical patent/JP2023548295A/ja
Publication of JP2023548295A5 publication Critical patent/JP2023548295A5/ja
Pending legal-status Critical Current

Links

JP2023525517A 2020-11-06 2021-11-05 修飾されたsiRNAを含む標的化コンジュゲート Pending JP2023548295A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063110837P 2020-11-06 2020-11-06
US63/110,837 2020-11-06
PCT/US2021/058232 WO2022098990A1 (en) 2020-11-06 2021-11-05 Targeted conjugates comprising modified sirna

Publications (2)

Publication Number Publication Date
JP2023548295A JP2023548295A (ja) 2023-11-16
JP2023548295A5 true JP2023548295A5 (https=) 2024-11-13

Family

ID=81457390

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023525517A Pending JP2023548295A (ja) 2020-11-06 2021-11-05 修飾されたsiRNAを含む標的化コンジュゲート

Country Status (11)

Country Link
US (1) US20240052349A1 (https=)
EP (1) EP4240369A4 (https=)
JP (1) JP2023548295A (https=)
KR (1) KR20230104652A (https=)
CN (1) CN116472063A (https=)
AU (1) AU2021376390A1 (https=)
CA (1) CA3199757A1 (https=)
IL (1) IL302530A (https=)
MX (1) MX2023005138A (https=)
TW (1) TW202233243A (https=)
WO (1) WO2022098990A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3020585A1 (en) * 2016-04-11 2017-10-19 Arbutus Biopharma Corporation Targeted nucleic acid conjugate compositions
WO2024099316A1 (zh) * 2022-11-08 2024-05-16 南京明德新药研发有限公司 含七元杂环的四价缀合基团及其应用
WO2026061476A1 (zh) * 2024-09-19 2026-03-26 长春金赛药业有限责任公司 一种多簇连接子、其制备方法及应用

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20050222064A1 (en) * 2002-02-20 2005-10-06 Sirna Therapeutics, Inc. Polycationic compositions for cellular delivery of polynucleotides
EP2563922A1 (en) * 2010-04-26 2013-03-06 Marina Biotech, Inc. Nucleic acid compounds with conformationally restricted monomers and uses thereof
CA2996722A1 (en) * 2015-07-17 2017-01-26 Arcturus Therapeutics, Inc. Compositions and agents against hepatitis b virus and uses thereof
CA3020585A1 (en) * 2016-04-11 2017-10-19 Arbutus Biopharma Corporation Targeted nucleic acid conjugate compositions
MX2019012280A (es) * 2017-04-11 2020-01-23 Arbutus Biopharma Corp Composiciones dirigidas.
US11324820B2 (en) * 2017-04-18 2022-05-10 Alnylam Pharmaceuticals, Inc. Methods for the treatment of subjects having a hepatitis b virus (HBV) infection
JP7473472B2 (ja) * 2017-10-17 2024-04-23 アローヘッド ファーマシューティカルズ インコーポレイテッド アシアロ糖タンパク質受容体1の発現を阻害するためのRNAi剤および組成物
MA55375A (fr) * 2019-03-20 2022-01-26 Arbutus Biopharma Corp Méthodes thérapeutiques de traitement de l'hépatite b

Similar Documents

Publication Publication Date Title
JP2023548295A5 (https=)
CN100400045C (zh) 基于核酸的化合物及其使用方法
JP2026062680A (ja) 核酸のデリバリーのための新規脂質および脂質ナノ粒子製剤
JP2021534124A5 (https=)
JP2023536320A5 (https=)
IL301757A (en) Cystic fibrosis transmembrane regulator conductance modulators
JP2011500758A5 (https=)
JP2006502143A5 (https=)
JP2007529421A5 (https=)
JP2015501833A5 (https=)
JP2012523415A5 (https=)
JP2018520685A5 (https=)
JP2012158602A5 (https=)
JP2006507265A5 (https=)
JP2004537517A5 (https=)
JP2023509870A5 (https=)
JP2011509302A5 (https=)
JP2008506710A5 (https=)
JP2023505434A5 (https=)
JP2018506272A5 (https=)
CN114409554A (zh) 一种新型阳离子脂质化合物及其组合物和用途
JP2005517677A5 (https=)
JP2025500860A5 (https=)
JP2022544538A5 (https=)
JP2018532786A5 (https=)