JP2022520653A5 - - Google Patents

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Publication number
JP2022520653A5
JP2022520653A5 JP2021547792A JP2021547792A JP2022520653A5 JP 2022520653 A5 JP2022520653 A5 JP 2022520653A5 JP 2021547792 A JP2021547792 A JP 2021547792A JP 2021547792 A JP2021547792 A JP 2021547792A JP 2022520653 A5 JP2022520653 A5 JP 2022520653A5
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JP
Japan
Application number
JP2021547792A
Other languages
Japanese (ja)
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JPWO2020167593A5 (https=
JP2022520653A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/017129 external-priority patent/WO2020167593A1/en
Publication of JP2022520653A publication Critical patent/JP2022520653A/ja
Publication of JPWO2020167593A5 publication Critical patent/JPWO2020167593A5/ja
Publication of JP2022520653A5 publication Critical patent/JP2022520653A5/ja
Withdrawn legal-status Critical Current

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JP2021547792A 2019-02-12 2020-02-07 Cyp27a1の発現を阻害するための方法及び組成物 Withdrawn JP2022520653A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962804410P 2019-02-12 2019-02-12
US62/804,410 2019-02-12
PCT/US2020/017129 WO2020167593A1 (en) 2019-02-12 2020-02-07 Methods and compositions for inhibiting expression of cyp27a1

Publications (3)

Publication Number Publication Date
JP2022520653A JP2022520653A (ja) 2022-03-31
JPWO2020167593A5 JPWO2020167593A5 (https=) 2023-04-13
JP2022520653A5 true JP2022520653A5 (https=) 2023-04-13

Family

ID=69941447

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021547792A Withdrawn JP2022520653A (ja) 2019-02-12 2020-02-07 Cyp27a1の発現を阻害するための方法及び組成物

Country Status (13)

Country Link
US (1) US20220186229A1 (https=)
EP (1) EP3908661A1 (https=)
JP (1) JP2022520653A (https=)
KR (1) KR20210132661A (https=)
CN (1) CN113692444A (https=)
AU (1) AU2020221892A1 (https=)
BR (1) BR112021015651A2 (https=)
CA (1) CA3128059A1 (https=)
CL (2) CL2021002120A1 (https=)
IL (1) IL285367A (https=)
MX (1) MX2021009754A (https=)
SG (1) SG11202108532RA (https=)
WO (1) WO2020167593A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2024269205A1 (en) * 2023-05-11 2025-12-11 Keymed Biosciences (Us) Inc. Dsrna molecules for regulating masp2 gene activity

Family Cites Families (18)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PT1309726E (pt) 2000-03-30 2010-03-08 Whitehead Biomedical Inst Mediadores de interferência por rna específicos de sequência de rna
AU2002213489A1 (en) * 2000-10-13 2002-04-22 Genaissance Pharmaceuticals, Inc. Haplotypes of the cyp27a1 gene
US20040259247A1 (en) 2000-12-01 2004-12-23 Thomas Tuschl Rna interference mediating small rna molecules
US20050159378A1 (en) 2001-05-18 2005-07-21 Sirna Therapeutics, Inc. RNA interference mediated inhibition of Myc and/or Myb gene expression using short interfering nucleic acid (siNA)
JP2005508196A (ja) 2001-11-07 2005-03-31 アプレラ コーポレイション 核酸分析の汎用ヌクレオチド
US20070265220A1 (en) 2004-03-15 2007-11-15 City Of Hope Methods and compositions for the specific inhibition of gene expression by double-stranded RNA
WO2007030167A1 (en) 2005-09-02 2007-03-15 Nastech Pharmaceutical Company Inc. Modification of double-stranded ribonucleic acid molecules
JP2012504389A (ja) * 2008-09-22 2012-02-23 ダイセルナ ファーマシューティカルズ, インコーポレイテッド 修飾を有するdsRNAによる遺伝子発現の特異的な阻害のための組成物および方法
US8691971B2 (en) 2008-09-23 2014-04-08 Scott G. Petersen Self delivering bio-labile phosphate protected pro-oligos for oligonucleotide based therapeutics and mediating RNA interference
US20100249214A1 (en) 2009-02-11 2010-09-30 Dicerna Pharmaceuticals Multiplex dicer substrate rna interference molecules having joining sequences
AU2009336191B2 (en) 2008-12-18 2017-08-24 Novo Nordisk A/S Extended dicer substrate agents and methods for the specific inhibition of gene expression
US8927513B2 (en) 2009-07-07 2015-01-06 Alnylam Pharmaceuticals, Inc. 5′ phosphate mimics
WO2011133871A2 (en) 2010-04-22 2011-10-27 Alnylam Pharmaceuticals, Inc. 5'-end derivatives
JP2015501155A (ja) 2011-10-25 2015-01-15 アイシス ファーマシューティカルズ, インコーポレーテッド Gccr発現のアンチセンス調整
EP2928877B1 (en) 2012-12-06 2020-01-22 Merck Sharp & Dohme Corp. Disulfide masked prodrug compositions and methods
JP2017522046A (ja) 2014-06-06 2017-08-10 ソルスティス バイオロジクス,リミティッド 生物可逆的および生物不可逆的基を有するポリヌクレオチド構築物
JP7105065B2 (ja) * 2014-12-15 2022-07-22 ダイセルナ ファーマシューティカルズ, インコーポレイテッド リガンド修飾二本鎖核酸
KR101916583B1 (ko) * 2017-04-20 2018-11-07 가천대학교 산학협력단 칼피르조밉을 유효성분으로 함유하는 담석증의 예방 또는 치료용 약학적 조성물

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