JP2021527087A5 - - Google Patents

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Publication number
JP2021527087A5
JP2021527087A5 JP2020568984A JP2020568984A JP2021527087A5 JP 2021527087 A5 JP2021527087 A5 JP 2021527087A5 JP 2020568984 A JP2020568984 A JP 2020568984A JP 2020568984 A JP2020568984 A JP 2020568984A JP 2021527087 A5 JP2021527087 A5 JP 2021527087A5
Authority
JP
Japan
Prior art keywords
pharmaceutical composition
composition according
microrna
promoter
mir145
Prior art date
Application number
JP2020568984A
Other languages
English (en)
Japanese (ja)
Other versions
JPWO2019241624A5 (https=
JP2021527087A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/037174 external-priority patent/WO2019241624A1/en
Publication of JP2021527087A publication Critical patent/JP2021527087A/ja
Publication of JP2021527087A5 publication Critical patent/JP2021527087A5/ja
Publication of JPWO2019241624A5 publication Critical patent/JPWO2019241624A5/ja
Withdrawn legal-status Critical Current

Links

JP2020568984A 2018-06-14 2019-06-14 アンジェルマン症候群の処置におけるMIR−92aまたはMIR−145の使用 Withdrawn JP2021527087A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862684774P 2018-06-14 2018-06-14
US62/684,774 2018-06-14
PCT/US2019/037174 WO2019241624A1 (en) 2018-06-14 2019-06-14 Use of mir-92a or mir-145 in the treatment of angelman syndrome

Publications (3)

Publication Number Publication Date
JP2021527087A JP2021527087A (ja) 2021-10-11
JP2021527087A5 true JP2021527087A5 (https=) 2022-06-10
JPWO2019241624A5 JPWO2019241624A5 (https=) 2022-06-10

Family

ID=68839583

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2020568984A Withdrawn JP2021527087A (ja) 2018-06-14 2019-06-14 アンジェルマン症候群の処置におけるMIR−92aまたはMIR−145の使用

Country Status (10)

Country Link
US (2) US10704048B2 (https=)
EP (1) EP3793567A4 (https=)
JP (1) JP2021527087A (https=)
KR (1) KR20210040358A (https=)
CN (1) CN112739353A (https=)
AU (1) AU2019285298A1 (https=)
CA (1) CA3103267A1 (https=)
IL (1) IL279391A (https=)
MX (1) MX2020013667A (https=)
WO (1) WO2019241624A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2020002148A (es) * 2017-08-25 2020-07-20 Ovid Therapeutics Inc Vectores adenoasociados recombinantes.
MX2020013667A (es) 2018-06-14 2021-03-02 Ovid Therapeutics Inc Uso de mir-92a o mir-145 en el tratamiento del sindrome de angelman.
WO2020227604A1 (en) * 2019-05-08 2020-11-12 Nova Southeastern University Regulation of nucleotide excision repair (ner) by microrna for treatment of breast cancer
KR20230128001A (ko) * 2020-12-01 2023-09-01 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 엔젤만 증후군의 치료를 위한 조성물 및 이의 용도

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5752515A (en) 1996-08-21 1998-05-19 Brigham & Women's Hospital Methods and apparatus for image-guided ultrasound delivery of compounds through the blood-brain barrier
WO2006128245A1 (en) 2005-06-03 2006-12-07 Southern Adelaide Health Service-Flinders Medical Centre Targeting cells with altered microrna expression
EP1937151A4 (en) 2005-09-19 2011-07-06 Univ Columbia Systems and methods for opening of the blood-brain barrier of a subject using ultrasound
CN102676516B (zh) * 2011-03-17 2014-06-04 中国医学科学院肿瘤研究所 microRNA 145的新用途
WO2013056216A1 (en) * 2011-10-14 2013-04-18 New York University Micrornas and methods of using same
AU2013262709A1 (en) * 2012-05-16 2015-01-22 Rana Therapeutics, Inc. Compositions and methods for modulating MECP2 expression
ES2809199T3 (es) 2012-06-25 2021-03-03 Ionis Pharmaceuticals Inc Modulación de la expresión de UBE3A-ATS
HUE062186T2 (hu) * 2015-05-07 2023-09-28 Univ South Florida Módosított UBE3A gén az Angelman-szindróma génterápiás megközelítésére
US20190298843A1 (en) * 2015-05-11 2019-10-03 Purdue Research Foundation Ligand ionophore conjugates
IL256912B2 (en) * 2015-07-17 2024-01-01 Ovid Therapeutics Inc Methods of treating developmental disorders with gaboxadol
MX2020013667A (es) 2018-06-14 2021-03-02 Ovid Therapeutics Inc Uso de mir-92a o mir-145 en el tratamiento del sindrome de angelman.

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