JP2020526514A5 - - Google Patents

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Publication number
JP2020526514A5
JP2020526514A5 JP2020500131A JP2020500131A JP2020526514A5 JP 2020526514 A5 JP2020526514 A5 JP 2020526514A5 JP 2020500131 A JP2020500131 A JP 2020500131A JP 2020500131 A JP2020500131 A JP 2020500131A JP 2020526514 A5 JP2020526514 A5 JP 2020526514A5
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JP
Japan
Prior art keywords
immunosuppressant
composition
use according
months
sequence
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JP2020500131A
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English (en)
Japanese (ja)
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JP2020526514A (ja
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Priority claimed from PCT/US2018/040957 external-priority patent/WO2019010335A1/en
Publication of JP2020526514A publication Critical patent/JP2020526514A/ja
Publication of JP2020526514A5 publication Critical patent/JP2020526514A5/ja
Priority to JP2023108011A priority Critical patent/JP7670759B2/ja
Pending legal-status Critical Current

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JP2020500131A 2017-07-06 2018-07-05 ムコ多糖症i型を治療するための遺伝子治療 Pending JP2020526514A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023108011A JP7670759B2 (ja) 2017-07-06 2023-06-30 ムコ多糖症i型を治療するための遺伝子治療

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762529385P 2017-07-06 2017-07-06
US62/529,385 2017-07-06
US201762530614P 2017-07-10 2017-07-10
US62/530,614 2017-07-10
US201862616106P 2018-01-11 2018-01-11
US62/616,106 2018-01-11
PCT/US2018/040957 WO2019010335A1 (en) 2017-07-06 2018-07-05 AAV9 MEDIATED GENE THERAPY FOR TREATING MUCOPOLYSACCHARIDOSIS TYPE I

Related Child Applications (1)

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JP2023108011A Division JP7670759B2 (ja) 2017-07-06 2023-06-30 ムコ多糖症i型を治療するための遺伝子治療

Publications (2)

Publication Number Publication Date
JP2020526514A JP2020526514A (ja) 2020-08-31
JP2020526514A5 true JP2020526514A5 (OSRAM) 2021-08-12

Family

ID=63036365

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020500131A Pending JP2020526514A (ja) 2017-07-06 2018-07-05 ムコ多糖症i型を治療するための遺伝子治療
JP2023108011A Active JP7670759B2 (ja) 2017-07-06 2023-06-30 ムコ多糖症i型を治療するための遺伝子治療

Family Applications After (1)

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JP2023108011A Active JP7670759B2 (ja) 2017-07-06 2023-06-30 ムコ多糖症i型を治療するための遺伝子治療

Country Status (11)

Country Link
US (2) US11890329B2 (OSRAM)
EP (1) EP3676385A1 (OSRAM)
JP (2) JP2020526514A (OSRAM)
KR (2) KR20200053468A (OSRAM)
AU (1) AU2018298133A1 (OSRAM)
BR (1) BR112020000063A2 (OSRAM)
CA (1) CA3068328A1 (OSRAM)
IL (1) IL271780A (OSRAM)
MA (1) MA50016A (OSRAM)
SG (1) SG11201912631PA (OSRAM)
WO (1) WO2019010335A1 (OSRAM)

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