JP2020518269A5 - - Google Patents
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- Publication number
- JP2020518269A5 JP2020518269A5 JP2019560667A JP2019560667A JP2020518269A5 JP 2020518269 A5 JP2020518269 A5 JP 2020518269A5 JP 2019560667 A JP2019560667 A JP 2019560667A JP 2019560667 A JP2019560667 A JP 2019560667A JP 2020518269 A5 JP2020518269 A5 JP 2020518269A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- ciliopathy
- seq
- promoter
- vector according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025093546A JP2025120285A (ja) | 2017-05-05 | 2025-06-04 | 繊毛病のための遺伝子治療 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GBGB1707212.5A GB201707212D0 (en) | 2017-05-05 | 2017-05-05 | Gene therapy for ciliopathies |
| GB1707212.5 | 2017-05-05 | ||
| PCT/GB2018/051219 WO2018203092A1 (en) | 2017-05-05 | 2018-05-04 | Gene therapy for ciliopathies |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025093546A Division JP2025120285A (ja) | 2017-05-05 | 2025-06-04 | 繊毛病のための遺伝子治療 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020518269A JP2020518269A (ja) | 2020-06-25 |
| JP2020518269A5 true JP2020518269A5 (https=) | 2021-07-26 |
| JP7759174B2 JP7759174B2 (ja) | 2025-10-23 |
Family
ID=59065740
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019560667A Active JP7759174B2 (ja) | 2017-05-05 | 2018-05-04 | 繊毛病のための遺伝子治療 |
| JP2025093546A Pending JP2025120285A (ja) | 2017-05-05 | 2025-06-04 | 繊毛病のための遺伝子治療 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025093546A Pending JP2025120285A (ja) | 2017-05-05 | 2025-06-04 | 繊毛病のための遺伝子治療 |
Country Status (8)
| Country | Link |
|---|---|
| US (2) | US12171794B2 (https=) |
| EP (1) | EP3628011A1 (https=) |
| JP (2) | JP7759174B2 (https=) |
| CN (1) | CN110753559A (https=) |
| AU (1) | AU2018262427B2 (https=) |
| CA (1) | CA3060187A1 (https=) |
| GB (1) | GB201707212D0 (https=) |
| WO (1) | WO2018203092A1 (https=) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201707212D0 (en) | 2017-05-05 | 2017-06-21 | Ucl Business Plc | Gene therapy for ciliopathies |
| HUE065017T2 (hu) * | 2019-02-14 | 2024-04-28 | Ethris Gmbh | Poliribonukleotid ciliogenezisre gyakorolt hatásának elemzése |
| JP2022551739A (ja) * | 2019-10-17 | 2022-12-13 | ストライドバイオ，インコーポレイテッド | ニーマン・ピック病ｃ型の治療のためのアデノ随伴ウイルスベクター |
| GB202005641D0 (en) * | 2020-04-17 | 2020-06-03 | Ucl Business Plc | Gene therapy for bardet-biedl syndrome |
| CN116042719B (zh) * | 2022-12-28 | 2025-11-11 | 蓝图生物医药(广州)有限公司 | 一种重组腺相关病毒载体及其应用 |
| WO2025049923A2 (en) * | 2023-08-31 | 2025-03-06 | The Board Of Trustees Of The Leland Stanford Junior University | Novel treatments of ciliopathies |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6962788B2 (en) * | 2002-05-30 | 2005-11-08 | University Of Iowa Research Foundation | Identification of a gene causing the most common form of bardet-biedl syndrome and uses thereof |
| EP1989328A4 (en) * | 2006-02-23 | 2009-07-01 | Univ Johns Hopkins | BBS10 ASSOCIATED DIAGNOSTIC PROCEDURES AND REAGENTS FOR BARDET BIEDL SYNDROME |
| EP2394667A1 (en) * | 2010-06-10 | 2011-12-14 | Laboratorios Del Dr. Esteve, S.A. | Vectors and sequences for the treatment of diseases |
| EP2970972B1 (en) * | 2013-03-11 | 2018-08-15 | Fondazione Telethon | Mir-204 and mir-211 and uses thereof |
| GB201707212D0 (en) | 2017-05-05 | 2017-06-21 | Ucl Business Plc | Gene therapy for ciliopathies |
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2017
- 2017-05-05 GB GBGB1707212.5A patent/GB201707212D0/en not_active Ceased
-
2018
- 2018-05-04 CA CA3060187A patent/CA3060187A1/en active Pending
- 2018-05-04 EP EP18725584.9A patent/EP3628011A1/en active Pending
- 2018-05-04 AU AU2018262427A patent/AU2018262427B2/en active Active
- 2018-05-04 JP JP2019560667A patent/JP7759174B2/ja active Active
- 2018-05-04 WO PCT/GB2018/051219 patent/WO2018203092A1/en not_active Ceased
- 2018-05-04 US US16/610,883 patent/US12171794B2/en active Active
- 2018-05-04 CN CN201880029421.3A patent/CN110753559A/zh active Pending
-
2024
- 2024-11-05 US US18/937,430 patent/US20250057899A1/en active Pending
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2025
- 2025-06-04 JP JP2025093546A patent/JP2025120285A/ja active Pending