JP2019537446A5 - - Google Patents

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Publication number
JP2019537446A5
JP2019537446A5 JP2019524226A JP2019524226A JP2019537446A5 JP 2019537446 A5 JP2019537446 A5 JP 2019537446A5 JP 2019524226 A JP2019524226 A JP 2019524226A JP 2019524226 A JP2019524226 A JP 2019524226A JP 2019537446 A5 JP2019537446 A5 JP 2019537446A5
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JP
Japan
Prior art keywords
nucleic acid
sequence
composition
pharmaceutical composition
domain
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JP2019524226A
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English (en)
Japanese (ja)
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JP7338937B2 (ja
JP2019537446A (ja
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Priority claimed from PCT/KR2017/010897 external-priority patent/WO2018088694A2/ko
Publication of JP2019537446A publication Critical patent/JP2019537446A/ja
Publication of JP2019537446A5 publication Critical patent/JP2019537446A5/ja
Application granted granted Critical
Publication of JP7338937B2 publication Critical patent/JP7338937B2/ja
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JP2019524226A 2016-11-14 2017-09-28 人工的に操作されたsc機能制御システム Active JP7338937B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662421516P 2016-11-14 2016-11-14
US62/421,516 2016-11-14
PCT/KR2017/010897 WO2018088694A2 (ko) 2016-11-14 2017-09-28 인위적으로 조작된 sc 기능 조절 시스템

Publications (3)

Publication Number Publication Date
JP2019537446A JP2019537446A (ja) 2019-12-26
JP2019537446A5 true JP2019537446A5 (https=) 2020-11-12
JP7338937B2 JP7338937B2 (ja) 2023-09-05

Family

ID=62109586

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2019524226A Active JP7338937B2 (ja) 2016-11-14 2017-09-28 人工的に操作されたsc機能制御システム

Country Status (9)

Country Link
US (1) US12331086B2 (https=)
EP (2) EP3896162B1 (https=)
JP (1) JP7338937B2 (https=)
KR (2) KR102437228B1 (https=)
CN (1) CN110248957B (https=)
AU (1) AU2017358122B2 (https=)
BR (1) BR112019009725A2 (https=)
RU (2) RU2022105597A (https=)
WO (1) WO2018088694A2 (https=)

Families Citing this family (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2020536501A (ja) * 2017-09-28 2020-12-17 ツールゲン インコーポレイテッドToolgen Incorporated 遺伝子発現調節のための人為的なゲノム操作
US11572574B2 (en) 2017-09-28 2023-02-07 Toolgen Incorporated Artificial genome manipulation for gene expression regulation
EP3851528A4 (en) * 2018-09-12 2023-12-06 Institute for Basic Science COMPOSITION FOR INDUCATING DEATH OF CELLS HAVING MUTATED GENE AND METHOD FOR INDUCATING DEATH OF CELLS HAVING MODIFIED GENE USING THE COMPOSITION
GB201907882D0 (en) 2019-06-03 2019-07-17 Cyprus Foundation For Muscular Dystrophy Res Methods
EP3798301A1 (en) * 2019-09-25 2021-03-31 KWS SAAT SE & Co. KGaA Promoter repression
WO2021184021A1 (en) * 2020-03-13 2021-09-16 Codiak Biosciences, Inc. Extracellular vesicle-aso constructs targeting pmp22
CN114621922A (zh) * 2022-02-15 2022-06-14 中山大学附属第五医院 一种大鼠海绵体神经来源施旺细胞的提取纯化和培养方法
WO2025079278A1 (ja) * 2023-10-10 2025-04-17 国立大学法人 東京医科歯科大学 シャルコー・マリー・トゥース病の処置剤

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR100613038B1 (ko) * 2004-07-07 2006-08-16 공주대학교 산학협력단 염색체 17p11.2-p12 지역의 중복을 제외한 유전자돌연변이를 발병 원인으로 하는 CMT 질환의 진단방법및 진단키트
JP2010531638A (ja) 2007-06-12 2010-09-30 ケース ウエスタン リザーブ ユニバーシティ 標的化された細胞死
AU2013335451C1 (en) 2012-10-23 2024-07-04 Toolgen Incorporated Composition for cleaving a target DNA comprising a guide RNA specific for the target DNA and Cas protein-encoding nucleic acid or Cas protein, and use thereof
EP3031921B1 (en) * 2012-12-12 2025-03-12 The Broad Institute, Inc. Delivery, engineering and optimization of systems, methods and compositions for sequence manipulation and therapeutic applications
WO2014204724A1 (en) 2013-06-17 2014-12-24 The Broad Institute Inc. Delivery, engineering and optimization of tandem guide systems, methods and compositions for sequence manipulation
WO2015048577A2 (en) * 2013-09-27 2015-04-02 Editas Medicine, Inc. Crispr-related methods and compositions
CA2935032C (en) 2013-12-26 2024-01-23 The General Hospital Corporation Multiplex guide rnas
WO2015188056A1 (en) 2014-06-05 2015-12-10 Sangamo Biosciences, Inc. Methods and compositions for nuclease design
EP4194557A1 (en) * 2014-08-06 2023-06-14 Institute for Basic Science Genome editing using campylobacter jejuni crispr/cas system-derived rgen
IL310721B2 (en) 2015-10-23 2025-11-01 Harvard College Nucleobase editors and uses thereof

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