JP2020527335A5 - - Google Patents

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Publication number
JP2020527335A5
JP2020527335A5 JP2019569784A JP2019569784A JP2020527335A5 JP 2020527335 A5 JP2020527335 A5 JP 2020527335A5 JP 2019569784 A JP2019569784 A JP 2019569784A JP 2019569784 A JP2019569784 A JP 2019569784A JP 2020527335 A5 JP2020527335 A5 JP 2020527335A5
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JP
Japan
Prior art keywords
promoter
aav
sequence
seq
vector according
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JP2019569784A
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English (en)
Japanese (ja)
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JP2020527335A (ja
JP7766393B2 (ja
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Priority claimed from PCT/US2018/037592 external-priority patent/WO2018232149A1/en
Publication of JP2020527335A publication Critical patent/JP2020527335A/ja
Publication of JP2020527335A5 publication Critical patent/JP2020527335A5/ja
Priority to JP2023098376A priority Critical patent/JP2023116709A/ja
Application granted granted Critical
Publication of JP7766393B2 publication Critical patent/JP7766393B2/ja
Active legal-status Critical Current
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JP2019569784A 2017-06-14 2018-06-14 眼疾患のための遺伝子療法 Active JP7766393B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023098376A JP2023116709A (ja) 2017-06-14 2023-06-15 眼疾患のための遺伝子療法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201762519821P 2017-06-14 2017-06-14
US62/519,821 2017-06-14
PCT/US2018/037592 WO2018232149A1 (en) 2017-06-14 2018-06-14 Gene therapy for ocular disorders

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023098376A Division JP2023116709A (ja) 2017-06-14 2023-06-15 眼疾患のための遺伝子療法

Publications (3)

Publication Number Publication Date
JP2020527335A JP2020527335A (ja) 2020-09-10
JP2020527335A5 true JP2020527335A5 (https=) 2021-07-26
JP7766393B2 JP7766393B2 (ja) 2025-11-10

Family

ID=64660849

Family Applications (2)

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JP2019569784A Active JP7766393B2 (ja) 2017-06-14 2018-06-14 眼疾患のための遺伝子療法
JP2023098376A Pending JP2023116709A (ja) 2017-06-14 2023-06-15 眼疾患のための遺伝子療法

Family Applications After (1)

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JP2023098376A Pending JP2023116709A (ja) 2017-06-14 2023-06-15 眼疾患のための遺伝子療法

Country Status (4)

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US (1) US11827898B2 (https=)
EP (1) EP3638316A4 (https=)
JP (2) JP7766393B2 (https=)
WO (1) WO2018232149A1 (https=)

Families Citing this family (8)

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JP7766393B2 (ja) * 2017-06-14 2025-11-10 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア 眼疾患のための遺伝子療法
CN113795279B (zh) * 2019-03-04 2024-12-31 宾夕法尼亚州大学信托人 靶向akt通路的神经保护性基因疗法
AU2021337580B2 (en) * 2020-09-02 2023-09-07 4D Molecular Therapeutics Inc. Codon optimized REP1 genes and uses thereof
WO2022165313A1 (en) 2021-02-01 2022-08-04 Regenxbio Inc. Gene therapy for neuronal ceroid lipofuscinoses
CN113322281B (zh) * 2021-05-12 2024-01-05 成都金唯科生物科技有限公司 一种高效组织特异性表达rs1蛋白的重组腺相关病毒及应用
CA3257440A1 (en) * 2022-07-06 2024-01-11 Adverum Biotechnologies, Inc. COMPOSITIONS AND METHODS FOR THE TREATMENT OF ACHROMOTOPSY
CN116411024A (zh) * 2023-03-10 2023-07-11 上海泰昶生物技术有限公司 用于生产重组腺相关病毒的质粒系统
CN121046460A (zh) * 2024-05-31 2025-12-02 上海朗昇生物科技有限公司 用于治疗Prom1相关视网膜疾病的新型治疗药物

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