JP2019508051A5 - - Google Patents

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Publication number
JP2019508051A5
JP2019508051A5 JP2018548318A JP2018548318A JP2019508051A5 JP 2019508051 A5 JP2019508051 A5 JP 2019508051A5 JP 2018548318 A JP2018548318 A JP 2018548318A JP 2018548318 A JP2018548318 A JP 2018548318A JP 2019508051 A5 JP2019508051 A5 JP 2019508051A5
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JP
Japan
Prior art keywords
nucleotide sequence
cells
cell
grna
targeting domain
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JP2018548318A
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English (en)
Japanese (ja)
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JP2019508051A (ja
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Priority claimed from PCT/US2017/022377 external-priority patent/WO2017160890A1/en
Publication of JP2019508051A publication Critical patent/JP2019508051A/ja
Publication of JP2019508051A5 publication Critical patent/JP2019508051A5/ja
Priority to JP2023026918A priority Critical patent/JP2023075166A/ja
Pending legal-status Critical Current

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JP2018548318A 2016-03-14 2017-03-14 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物 Pending JP2019508051A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023026918A JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201662308190P 2016-03-14 2016-03-14
US62/308,190 2016-03-14
US201762456615P 2017-02-08 2017-02-08
US62/456,615 2017-02-08
PCT/US2017/022377 WO2017160890A1 (en) 2016-03-14 2017-03-14 Crispr/cas-related methods and compositions for treating beta hemoglobinopathies

Related Child Applications (1)

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JP2023026918A Division JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

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JP2019508051A JP2019508051A (ja) 2019-03-28
JP2019508051A5 true JP2019508051A5 (enExample) 2020-04-23

Family

ID=58413206

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JP2018548318A Pending JP2019508051A (ja) 2016-03-14 2017-03-14 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物
JP2023026918A Pending JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

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JP2023026918A Pending JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのCRISPR/CAS関連方法および組成物

Country Status (11)

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US (2) US20200255857A1 (enExample)
EP (1) EP3430142A1 (enExample)
JP (2) JP2019508051A (enExample)
KR (2) KR102723347B1 (enExample)
CN (4) CN109153994A (enExample)
AU (2) AU2017235333B2 (enExample)
CA (1) CA3017956A1 (enExample)
IL (2) IL313038A (enExample)
MX (2) MX2018011114A (enExample)
SG (1) SG11201807859WA (enExample)
WO (1) WO2017160890A1 (enExample)

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