JP2019508051A - β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物 - Google Patents

β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物 Download PDF

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JP2019508051A
JP2019508051A JP2018548318A JP2018548318A JP2019508051A JP 2019508051 A JP2019508051 A JP 2019508051A JP 2018548318 A JP2018548318 A JP 2018548318A JP 2018548318 A JP2018548318 A JP 2018548318A JP 2019508051 A JP2019508051 A JP 2019508051A
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nucleic acid
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nucleotides
molecule
hbg1
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JP2019508051A5 (enExample
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ゴリ、ジェニファー・リア
バレラ、ルイス・エー．
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エディタス・メディシン、インコーポレイテッド
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JP2018548318A 2016-03-14 2017-03-14 β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物 Pending JP2019508051A (ja)

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Application Number Priority Date Filing Date Title
JP2023026918A JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物
JP2025244943A JP2026064992A (ja) 2016-03-14 2025-12-11 β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201662308190P 2016-03-14 2016-03-14
US62/308,190 2016-03-14
US201762456615P 2017-02-08 2017-02-08
US62/456,615 2017-02-08
PCT/US2017/022377 WO2017160890A1 (en) 2016-03-14 2017-03-14 Crispr/cas-related methods and compositions for treating beta hemoglobinopathies

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JP2023026918A Pending JP2023075166A (ja) 2016-03-14 2023-02-24 β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物
JP2025244943A Pending JP2026064992A (ja) 2016-03-14 2025-12-11 β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物

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JP2025244943A Pending JP2026064992A (ja) 2016-03-14 2025-12-11 β異常ヘモグロビン症を治療するためのＣＲＩＳＰＲ／ＣＡＳ関連方法および組成物

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KR (2) KR102532663B1 (enExample)
CN (4) CN118127006A (enExample)
AU (3) AU2017235333B2 (enExample)
CA (1) CA3017956A1 (enExample)
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Cited By (2)

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JP2023530969A (ja) * 2020-07-01 2023-07-20 広州瑞風生物科技有限公司 γ－グロビン遺伝子発現を活性化する方法、および組成物
JP2024528967A (ja) * 2021-08-02 2024-08-01 エディタス・メディシン、インコーポレイテッド ヘモグロビン異常症の治療のためのシステム及び方法

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