JP2018531609A5 - - Google Patents

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Publication number
JP2018531609A5
JP2018531609A5 JP2018521395A JP2018521395A JP2018531609A5 JP 2018531609 A5 JP2018531609 A5 JP 2018531609A5 JP 2018521395 A JP2018521395 A JP 2018521395A JP 2018521395 A JP2018521395 A JP 2018521395A JP 2018531609 A5 JP2018531609 A5 JP 2018531609A5
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JP
Japan
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nucleic acid
seq
vector
sequence
fxn
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JP2018521395A
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English (en)
Japanese (ja)
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JP6767483B2 (ja
JP2018531609A (ja
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Priority claimed from PCT/IB2016/056572 external-priority patent/WO2017077451A1/en
Publication of JP2018531609A publication Critical patent/JP2018531609A/ja
Publication of JP2018531609A5 publication Critical patent/JP2018531609A5/ja
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Publication of JP6767483B2 publication Critical patent/JP6767483B2/ja
Expired - Fee Related legal-status Critical Current
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JP2018521395A 2015-11-05 2016-11-01 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター Expired - Fee Related JP6767483B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562251288P 2015-11-05 2015-11-05
US62/251,288 2015-11-05
US201662411980P 2016-10-24 2016-10-24
US62/411,980 2016-10-24
PCT/IB2016/056572 WO2017077451A1 (en) 2015-11-05 2016-11-01 Modified friedreich ataxia genes and vectors for gene therapy

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2020156320A Division JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

Publications (3)

Publication Number Publication Date
JP2018531609A JP2018531609A (ja) 2018-11-01
JP2018531609A5 true JP2018531609A5 (OSRAM) 2019-12-12
JP6767483B2 JP6767483B2 (ja) 2020-10-14

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ID=57288476

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JP2018521395A Expired - Fee Related JP6767483B2 (ja) 2015-11-05 2016-11-01 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター
JP2020156320A Pending JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

Family Applications After (1)

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JP2020156320A Pending JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

Country Status (18)

Country Link
US (2) US10548947B2 (OSRAM)
EP (1) EP3370778A1 (OSRAM)
JP (2) JP6767483B2 (OSRAM)
KR (2) KR20210005994A (OSRAM)
CN (1) CN108348621A (OSRAM)
AU (2) AU2016347887B2 (OSRAM)
BR (1) BR112018007453A2 (OSRAM)
CA (1) CA2947584A1 (OSRAM)
CO (1) CO2018004564A2 (OSRAM)
HK (1) HK1250924A1 (OSRAM)
IL (1) IL259141A (OSRAM)
MX (1) MX2018005084A (OSRAM)
PE (1) PE20181156A1 (OSRAM)
PH (1) PH12018500964A1 (OSRAM)
RU (2) RU2021102893A (OSRAM)
SG (2) SG11201802408RA (OSRAM)
TW (2) TWI654301B (OSRAM)
WO (1) WO2017077451A1 (OSRAM)

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