IL256517B2 - Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues - Google Patents
Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissuesInfo
- Publication number
- IL256517B2 IL256517B2 IL256517A IL25651717A IL256517B2 IL 256517 B2 IL256517 B2 IL 256517B2 IL 256517 A IL256517 A IL 256517A IL 25651717 A IL25651717 A IL 25651717A IL 256517 B2 IL256517 B2 IL 256517B2
- Authority
- IL
- Israel
- Prior art keywords
- sequence
- seq
- nucleic acid
- aav
- raav vector
- Prior art date
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| EP2357010B1 (en) * | 2005-04-07 | 2013-06-12 | The Trustees of The University of Pennsylvania | Method of increasing the function of an AAV vector |
| HUE067487T2 (hu) | 2008-09-15 | 2024-10-28 | Uniqure Biopharma B V | IX-es faktor polipeptid mutánsa, alkalmazásai és eljárás az elõállítására |
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