EA201991455A1 - Композиции и способы лечения дефицита альфа-1-антитрипсина - Google Patents

Композиции и способы лечения дефицита альфа-1-антитрипсина

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Publication number
EA201991455A1
EA201991455A1 EA201991455A EA201991455A EA201991455A1 EA 201991455 A1 EA201991455 A1 EA 201991455A1 EA 201991455 A EA201991455 A EA 201991455A EA 201991455 A EA201991455 A EA 201991455A EA 201991455 A1 EA201991455 A1 EA 201991455A1
Authority
EA
Eurasian Patent Office
Prior art keywords
compositions
methods
deficiency
antitripsin
treating alpha
Prior art date
Application number
EA201991455A
Other languages
English (en)
Russian (ru)
Inventor
Сёбу Одате
Уолтер Стрэппс
Рейнальд Майкл Лескарбо
Original Assignee
Интеллиа Терапьютикс, Инк.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Интеллиа Терапьютикс, Инк. filed Critical Интеллиа Терапьютикс, Инк.
Publication of EA201991455A1 publication Critical patent/EA201991455A1/ru

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    • C12N15/09—Recombinant DNA-technology
    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • A—HUMAN NECESSITIES
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    • A61K47/00—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient
    • A61K47/06—Organic compounds, e.g. natural or synthetic hydrocarbons, polyolefins, mineral oil, petrolatum or ozokerite
    • A61K47/24—Organic compounds, e.g. natural or synthetic hydrocarbons, polyolefins, mineral oil, petrolatum or ozokerite containing atoms other than carbon, hydrogen, oxygen, halogen, nitrogen or sulfur, e.g. cyclomethicone or phospholipids
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EA201991455A 2016-12-22 2017-12-21 Композиции и способы лечения дефицита альфа-1-антитрипсина EA201991455A1 (ru)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201662438219P 2016-12-22 2016-12-22
PCT/US2017/067800 WO2018119182A1 (en) 2016-12-22 2017-12-21 Compositions and methods for treating alpha-1 antitrypsin deficiency

Publications (1)

Publication Number Publication Date
EA201991455A1 true EA201991455A1 (ru) 2020-01-15

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Country Link
US (2) US11549107B2 (https=)
EP (1) EP3559232A1 (https=)
JP (2) JP7383478B2 (https=)
KR (1) KR102551664B1 (https=)
CN (2) CN110382697B (https=)
AU (2) AU2017379073B2 (https=)
BR (1) BR112019012825A2 (https=)
CA (1) CA3047415A1 (https=)
CO (1) CO2019007776A2 (https=)
EA (1) EA201991455A1 (https=)
IL (1) IL267448B2 (https=)
MX (2) MX2019007594A (https=)
MY (1) MY204487A (https=)
PH (1) PH12019501457A1 (https=)
SA (1) SA519402192B1 (https=)
SG (1) SG10202106412RA (https=)
TW (2) TWI851534B (https=)
WO (1) WO2018119182A1 (https=)
ZA (1) ZA202007632B (https=)

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CN110382697B (zh) 2023-12-29
KR102551664B1 (ko) 2023-07-05
IL267448B2 (en) 2025-09-01
ZA202007632B (en) 2023-03-29
CA3047415A1 (en) 2018-06-28
CN117737062A (zh) 2024-03-22
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US12460205B2 (en) 2025-11-04
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