KR102551664B1 - 알파-1 항트립신 결핍을 치료하기 위한 조성물 및 방법 - Google Patents

알파-1 항트립신 결핍을 치료하기 위한 조성물 및 방법 Download PDF

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KR102551664B1
KR102551664B1 KR1020197020995A KR20197020995A KR102551664B1 KR 102551664 B1 KR102551664 B1 KR 102551664B1 KR 1020197020995 A KR1020197020995 A KR 1020197020995A KR 20197020995 A KR20197020995 A KR 20197020995A KR 102551664 B1 KR102551664 B1 KR 102551664B1
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쇼부 오다테
왈터 스트랩스
레이날드 미카엘 레스카뷰
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인텔리아 테라퓨틱스, 인크.
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KR1020197020995A 2016-12-22 2017-12-21 알파-1 항트립신 결핍을 치료하기 위한 조성물 및 방법 Active KR102551664B1 (ko)

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Application Number Priority Date Filing Date Title
US201662438219P 2016-12-22 2016-12-22
US62/438,219 2016-12-22
PCT/US2017/067800 WO2018119182A1 (en) 2016-12-22 2017-12-21 Compositions and methods for treating alpha-1 antitrypsin deficiency

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KR20190100943A KR20190100943A (ko) 2019-08-29
KR102551664B1 true KR102551664B1 (ko) 2023-07-05

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US (2) US11549107B2 (https=)
EP (1) EP3559232A1 (https=)
JP (2) JP7383478B2 (https=)
KR (1) KR102551664B1 (https=)
CN (2) CN110382697B (https=)
AU (2) AU2017379073B2 (https=)
BR (1) BR112019012825A2 (https=)
CA (1) CA3047415A1 (https=)
CO (1) CO2019007776A2 (https=)
EA (1) EA201991455A1 (https=)
IL (1) IL267448B2 (https=)
MX (2) MX2019007594A (https=)
MY (1) MY204487A (https=)
PH (1) PH12019501457A1 (https=)
SA (1) SA519402192B1 (https=)
SG (1) SG10202106412RA (https=)
TW (2) TWI851534B (https=)
WO (1) WO2018119182A1 (https=)
ZA (1) ZA202007632B (https=)

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JP7578590B2 (ja) 2018-10-18 2024-11-06 インテリア セラピューティクス，インコーポレーテッド 第ｉｘ因子を発現するための組成物及び方法
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WO2022060707A1 (en) * 2020-09-15 2022-03-24 Rutgers, The State University Of New Jersey Systems for gene editing and methods of use thereof
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US20220160847A1 (en) * 2020-11-20 2022-05-26 Mark Egly Method of preventing and/or treating a plurality of diseases
CR20230305A (es) 2020-12-11 2023-11-10 Intellia Therapeutics Inc Polinucleótidos, composiciones y métodos para la edición del genoma que implican desaminación
EP4288541A1 (en) 2021-02-05 2023-12-13 Christiana Care Gene Editing Institute, Inc. Methods of and compositions for reducing gene expression and/or activity
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