CN116194154A - 使用aav载体的plakophilin-2(pkp2)基因疗法 - Google Patents

使用aav载体的plakophilin-2(pkp2)基因疗法 Download PDF

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Publication number
CN116194154A
CN116194154A CN202180058096.5A CN202180058096A CN116194154A CN 116194154 A CN116194154 A CN 116194154A CN 202180058096 A CN202180058096 A CN 202180058096A CN 116194154 A CN116194154 A CN 116194154A
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vector
polynucleotide
ser
gly
leu
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C·D·赫尔佐格
C·B·萨克拉门多
R·普拉巴卡尔
D·里克斯
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Spaceship Seven LLC
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CN202180058096.5A 2020-08-07 2021-08-09 使用aav载体的plakophilin-2(pkp2)基因疗法 Pending CN116194154A (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063063032P 2020-08-07 2020-08-07
US63/063,032 2020-08-07
PCT/US2021/045220 WO2022032226A1 (en) 2020-08-07 2021-08-09 Plakophilin-2 (pkp2) gene therapy using aav vector

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CN116194154A true CN116194154A (zh) 2023-05-30

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US (4) US11883506B2 (enExample)
EP (1) EP4192487A4 (enExample)
JP (1) JP2023538519A (enExample)
KR (1) KR20230043869A (enExample)
CN (1) CN116194154A (enExample)
AU (1) AU2021320902A1 (enExample)
BR (1) BR112023001852A2 (enExample)
CA (1) CA3185267A1 (enExample)
IL (1) IL300263A (enExample)
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