CN112041437A - 用于恢复f8基因功能的腺相关病毒组合物和其使用方法 - Google Patents

用于恢复f8基因功能的腺相关病毒组合物和其使用方法 Download PDF

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Publication number
CN112041437A
CN112041437A CN201980025614.6A CN201980025614A CN112041437A CN 112041437 A CN112041437 A CN 112041437A CN 201980025614 A CN201980025614 A CN 201980025614A CN 112041437 A CN112041437 A CN 112041437A
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amino acid
seq
capsid protein
protein corresponding
gly
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Chinese (zh)
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S.查特吉
L.J.史密斯
J.L.埃尔斯沃思
H.鲁宾
J.B.赖特
J.A.麦克斯维甘
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City of Hope
Cognate3 LLC
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City of Hope
Cognate3 LLC
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CN201980025614.6A 2018-02-19 2019-02-19 用于恢复f8基因功能的腺相关病毒组合物和其使用方法 Pending CN112041437A (zh)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201862632300P 2018-02-19 2018-02-19
US62/632,300 2018-02-19
US201862632919P 2018-02-20 2018-02-20
US62/632,919 2018-02-20
US201862672385P 2018-05-16 2018-05-16
US62/672,385 2018-05-16
PCT/US2019/018502 WO2019161365A1 (en) 2018-02-19 2019-02-19 Adeno-associated virus compositions for restoring f8 gene function and methods of use thereof

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CN112041437A true CN112041437A (zh) 2020-12-04

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US (2) US11306329B2 (https=)
EP (1) EP3755795A4 (https=)
JP (1) JP7244547B2 (https=)
CN (1) CN112041437A (https=)
WO (1) WO2019161365A1 (https=)

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* Cited by examiner, † Cited by third party
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WO2022241041A2 (en) * 2021-05-11 2022-11-17 City Of Hope Adeno-associated virus compositions and methods of use thereof
WO2024229281A1 (en) * 2023-05-02 2024-11-07 City Of Hope Adeno-associated virus compositions and methods of use thereof

Citations (1)

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