CN107438671B - 变体RNAi - Google Patents

变体RNAi Download PDF

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Publication number
CN107438671B
CN107438671B CN201680020699.5A CN201680020699A CN107438671B CN 107438671 B CN107438671 B CN 107438671B CN 201680020699 A CN201680020699 A CN 201680020699A CN 107438671 B CN107438671 B CN 107438671B
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vector
rnai
aav
strand
promoter
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CN107438671A (zh
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L·M·施塔内克
A·巴勒莫
B·理查兹
S·P·萨尔迪
C·奥赖尔登
A·宋
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Genzyme Corp
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Genzyme Corp
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CN201680020699.5A 2015-02-10 2016-02-09 变体RNAi Active CN107438671B (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562114578P 2015-02-10 2015-02-10
US62/114,578 2015-02-10
PCT/US2016/017207 WO2016130589A2 (en) 2015-02-10 2016-02-09 VARIANT RNAi

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CN107438671A CN107438671A (zh) 2017-12-05
CN107438671B true CN107438671B (zh) 2021-05-25

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EP (1) EP3256588A2 (enExample)
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KR (1) KR102670852B1 (enExample)
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AR (1) AR103646A1 (enExample)
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