CN104718295B - 用于治疗奥尔波特综合征的方法 - Google Patents

用于治疗奥尔波特综合征的方法 Download PDF

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CN104718295B
CN104718295B CN201380051249.9A CN201380051249A CN104718295B CN 104718295 B CN104718295 B CN 104718295B CN 201380051249 A CN201380051249 A CN 201380051249A CN 104718295 B CN104718295 B CN 104718295B
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certain embodiments
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nucleosides
syndrome
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CN104718295A (zh
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J·达菲尔德
B·巴特
D·麦肯纳
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Sanofi Aventis France
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Sanofi Aventis France
Regulus Therapeutics Inc
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    • C12N2310/30—Chemical structure
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    • C12N2310/323—Chemical structure of the sugar modified ring structure
    • C12N2310/3233—Morpholino-type ring

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CN201380051249.9A 2012-10-09 2013-10-08 用于治疗奥尔波特综合征的方法 Active CN104718295B (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201261711514P 2012-10-09 2012-10-09
US61/711,514 2012-10-09
US201361779137P 2013-03-13 2013-03-13
US61/779,137 2013-03-13
PCT/US2013/063884 WO2014058881A1 (en) 2012-10-09 2013-10-08 Methods for treatment of alport syndrome

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CN104718295A CN104718295A (zh) 2015-06-17
CN104718295B true CN104718295B (zh) 2020-03-13

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AU (3) AU2013329427B2 (https=)
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