CA2829947C - Dosing regimens for the treatment of fabry disease - Google Patents
Dosing regimens for the treatment of fabry disease Download PDFInfo
- Publication number
- CA2829947C CA2829947C CA2829947A CA2829947A CA2829947C CA 2829947 C CA2829947 C CA 2829947C CA 2829947 A CA2829947 A CA 2829947A CA 2829947 A CA2829947 A CA 2829947A CA 2829947 C CA2829947 C CA 2829947C
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- Canada
- Prior art keywords
- gal
- deoxygalactonojirimycin
- agalsidase
- salt
- migalastat
- Prior art date
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| EP4541418A3 (en) | 2006-05-16 | 2025-07-09 | Amicus Therapeutics, Inc. | Assays for diagnosing and evaluating treatment options for fabry disease |
| PL2252313T3 (pl) | 2008-02-12 | 2015-09-30 | Amicus Therapeutics Inc | Sposób przewidywania odpowiedzi na leczenie chorób farmakologicznymi białkami chaperonowymi |
| UY34317A (es) | 2011-09-12 | 2013-02-28 | Genzyme Corp | Anticuerpo antireceptor de célula T (alfa)/ß |
| US9790268B2 (en) | 2012-09-12 | 2017-10-17 | Genzyme Corporation | Fc containing polypeptides with altered glycosylation and reduced effector function |
| WO2014164503A1 (en) | 2013-03-11 | 2014-10-09 | Genzyme Corporation | Hyperglycosylated binding polypeptides |
| RU2016137120A (ru) * | 2014-02-17 | 2018-03-22 | Глэксосмитклайн Интеллекчуал Проперти Дивелопмент Лимитед | Микробиологический способ |
| CN116333148A (zh) | 2014-03-19 | 2023-06-27 | 建新公司 | 靶向模块的位点特异性糖工程化 |
| US9675627B2 (en) * | 2014-04-14 | 2017-06-13 | Amicus Therapeutics, Inc. | Dosing regimens for treating and/or preventing cerebral amyloidoses |
| US10874355B2 (en) | 2014-04-24 | 2020-12-29 | Cognoa, Inc. | Methods and apparatus to determine developmental progress with artificial intelligence and user input |
| GB201508025D0 (en) * | 2015-05-11 | 2015-06-24 | Ucl Business Plc | Fabry disease gene therapy |
| US11972336B2 (en) | 2015-12-18 | 2024-04-30 | Cognoa, Inc. | Machine learning platform and system for data analysis |
| EP3432882B1 (en) * | 2016-03-22 | 2021-09-01 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having the g9331a mutation in the gla gene |
| US12070453B2 (en) * | 2016-07-19 | 2024-08-27 | Amicus Therapeutics, Inc. | Treatment of Fabry disease in ERT-naïve and ERT-experienced patients |
| JP7182554B2 (ja) | 2016-11-14 | 2022-12-02 | コグノア，インク． | 発達に係る疾病を評価し、およびカバー率と信頼度に対する制御を提供する方法および装置 |
| WO2018148365A1 (en) * | 2017-02-09 | 2018-08-16 | Cognoa, Inc. | Platform and system for digital personalized medicine |
| MX391565B (es) | 2017-05-30 | 2025-03-21 | Amicus Therapeutics Inc | Métodos de tratamiento de pacientes con enfermedad de fabry que tienen insuficiencia renal. |
| TWI795408B (zh) * | 2017-05-30 | 2023-03-11 | 美商阿米庫斯醫療股份有限公司 | 治療有腎損傷的法布里患者的方法 |
| JP7066157B2 (ja) | 2017-06-14 | 2022-05-13 | 学校法人 明治薬科大学 | ファブリー病治療用医薬の組合せ物及びその利用 |
| KR20200128676A (ko) | 2018-02-06 | 2020-11-16 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 임신 환자의 파브리병 치료를 위한 미갈라스타트의 용도 |
| CA3110065A1 (en) * | 2018-08-20 | 2020-02-27 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having a mutation in the gla gene |
| CN113873935B (zh) | 2019-03-22 | 2024-11-22 | 科格诺亚公司 | 个性化数字化治疗方法和装置 |
| WO2020206063A1 (en) | 2019-04-03 | 2020-10-08 | Genzyme Corporation | Anti-alpha beta tcr binding polypeptides with reduced fragmentation |
| EA202290024A1 (ru) * | 2019-06-11 | 2022-03-14 | Амикус Терапьютикс, Инк. | Способы лечения болезни фабри у пациентов с почечной недостаточностью |
| EP3851105A3 (en) | 2019-08-07 | 2021-10-13 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having a mutation in the gla gene |
| US11623916B2 (en) | 2020-12-16 | 2023-04-11 | Amicus Therapeutics, Inc. | Highly purified batches of pharmaceutical grade migalastat and methods of producing the same |
| US20240120050A1 (en) * | 2022-10-07 | 2024-04-11 | Insight Direct Usa, Inc. | Machine learning method for predicting a health outcome of a patient using video and audio analytics |
| US20240197706A1 (en) * | 2022-12-13 | 2024-06-20 | Amicus Therapeutics, Inc. | Methods of improving the pharmacokinetics of migalastat |
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| US6274597B1 (en) * | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| ES2531478T3 (es) * | 2003-01-31 | 2015-03-16 | The Mount Sinai School Of Medicine Of New York University | Terapia de combinación para tratar trastornos de deficiencia de proteínas |
| US7879354B2 (en) * | 2004-01-13 | 2011-02-01 | Mcneil-Ppc, Inc. | Rapidly disintegrating gelatinous coated tablets |
| CN100457106C (zh) * | 2005-06-15 | 2009-02-04 | 同济大学 | 1-脱氧野尻霉素在制备治疗糖尿病肾病药物中的应用 |
| EP4541418A3 (en) * | 2006-05-16 | 2025-07-09 | Amicus Therapeutics, Inc. | Assays for diagnosing and evaluating treatment options for fabry disease |
| WO2008121826A2 (en) * | 2007-03-30 | 2008-10-09 | Amicus Therapeutics, Inc. | Method for the treatment of fabry disease using pharmacological chaperones |
| MX2009011473A (es) * | 2007-04-26 | 2010-01-18 | Amicus Therapeutics Inc | Regimenes de dosificacion para el tratamiento de enfermedades por almacenamiento lisosomal que utilizan chaperonas farmacologicas. |
| US20100291060A1 (en) * | 2007-08-29 | 2010-11-18 | Shire Human Genetic Therapies, Inc | Subcutaneous administration of alpha-galactosidase a |
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