AU2019215152A1 - Adeno-associated virus compositions for restoring PAH gene function and methods of use thereof - Google Patents
Adeno-associated virus compositions for restoring PAH gene function and methods of use thereof Download PDFInfo
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- AU2019215152A1 AU2019215152A1 AU2019215152A AU2019215152A AU2019215152A1 AU 2019215152 A1 AU2019215152 A1 AU 2019215152A1 AU 2019215152 A AU2019215152 A AU 2019215152A AU 2019215152 A AU2019215152 A AU 2019215152A AU 2019215152 A1 AU2019215152 A1 AU 2019215152A1
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- amino acid
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- capsid protein
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| PCT/US2019/016354 WO2019152843A1 (en) | 2018-02-01 | 2019-02-01 | Adeno-associated virus compositions for restoring pah gene function and methods of use thereof |
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| JP2023510392A (ja) * | 2020-01-16 | 2023-03-13 | 武田薬品工業株式会社 | フェニルケトン尿症に対するアデノ随伴ウイルスベースの遺伝子治療 |
| IL296986A (en) * | 2020-04-06 | 2022-12-01 | Homology Medicines Inc | Adeno-associated virus preparations for ids gene transfer and methods of use thereof |
| TW202208632A (zh) | 2020-05-27 | 2022-03-01 | 美商同源醫藥公司 | 用於恢復ｐａｈ基因功能的腺相關病毒組成物及其使用方法 |
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| DE4407859C1 (de) | 1994-03-04 | 1995-03-02 | Max Planck Gesellschaft | Vektor für die leberspezifische Gentherapie |
| ATE386131T1 (de) | 1994-04-13 | 2008-03-15 | Univ Rockefeller | Aav-vermittelte überbringung von dna in zellen des nervensystems |
| AU3718595A (en) | 1994-09-16 | 1996-03-29 | Uab Research Foundation, The | Transduction of genes into human hematopoietic stem cells using recombinant adeno-associated viral vectors |
| JPH10506530A (ja) | 1994-09-23 | 1998-06-30 | ザ ジェネラル ホスピタル コーポレーション | 哺乳類細胞において外来遺伝子を発現する非哺乳類ｄｎａウイルスの使用 |
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| DE19525900C1 (de) | 1995-07-15 | 1996-12-12 | Max Planck Gesellschaft | Leberspezifischer Adenovirus-Expressionsvektor |
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2019
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| US20190256867A1 (en) | 2019-08-22 |
| PE20212076A1 (es) | 2021-10-26 |
| KR20200127170A (ko) | 2020-11-10 |
| MX2020008133A (es) | 2020-10-14 |
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