AU2018309187C1 - Methods and compositions for modulating splicing - Google Patents

Methods and compositions for modulating splicing Download PDF

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AU2018309187C1
AU2018309187C1 AU2018309187A AU2018309187A AU2018309187C1 AU 2018309187 C1 AU2018309187 C1 AU 2018309187C1 AU 2018309187 A AU2018309187 A AU 2018309187A AU 2018309187 A AU2018309187 A AU 2018309187A AU 2018309187 C1 AU2018309187 C1 AU 2018309187C1
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substituted
unsubstituted
alkyl
ring
heteroaryl
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AU2018309187A1 (en
AU2018309187B2 (en
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William Haney
Michael Luzzio
Kathleen Mccarthy
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Skyhawk Therapeutics Inc
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Skyhawk Therapeutics Inc
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AU2018309187A 2017-08-04 2018-08-03 Methods and compositions for modulating splicing Active AU2018309187C1 (en)

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US201762541202P 2017-08-04 2017-08-04
US62/541,202 2017-08-04
US201762562948P 2017-09-25 2017-09-25
US201762562927P 2017-09-25 2017-09-25
US62/562,927 2017-09-25
US62/562,948 2017-09-25
PCT/US2018/045282 WO2019028440A1 (en) 2017-08-04 2018-08-03 METHODS AND COMPOSITIONS FOR MODULATING SPLICING

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EP (2) EP3661509A4 (https=)
JP (2) JP7312749B2 (https=)
KR (2) KR102636384B1 (https=)
CN (2) CN111194215B (https=)
AU (2) AU2018309187C1 (https=)
CA (1) CA3072205A1 (https=)
GB (2) GB2587457B (https=)
IL (2) IL273741B (https=)
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EA201800367A1 (ru) 2015-12-10 2019-02-28 ПиТиСи ТЕРАПЬЮТИКС, ИНК. Способы лечения болезни хантингтона
JP2019535789A (ja) 2016-11-28 2019-12-12 ピーティーシー セラピューティクス，インコーポレーテッド Ｒｎａスプライシングを調節する方法
EP3634953B1 (en) 2017-06-05 2024-01-03 PTC Therapeutics, Inc. Compounds for treating huntington's disease
JP2020523365A (ja) 2017-06-14 2020-08-06 ピーティーシー セラピューティクス，インコーポレーテッド Ｒｎａスプライシングを改変する方法
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