ZA202007632B - Compositions and methods for treating alpha-1 antitrypsin deficiency - Google Patents

Compositions and methods for treating alpha-1 antitrypsin deficiency

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Publication number
ZA202007632B
ZA202007632B ZA2020/07632A ZA202007632A ZA202007632B ZA 202007632 B ZA202007632 B ZA 202007632B ZA 2020/07632 A ZA2020/07632 A ZA 2020/07632A ZA 202007632 A ZA202007632 A ZA 202007632A ZA 202007632 B ZA202007632 B ZA 202007632B
Authority
ZA
South Africa
Prior art keywords
compositions
methods
antitrypsin deficiency
treating alpha
alpha
Prior art date
Application number
ZA2020/07632A
Other languages
English (en)
Inventor
Walter Strapps
Shobu Odate
Reynald Michael Lescarbeau
Original Assignee
Intellia Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Intellia Therapeutics Inc filed Critical Intellia Therapeutics Inc
Publication of ZA202007632B publication Critical patent/ZA202007632B/en

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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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ZA2020/07632A 2016-12-22 2020-12-08 Compositions and methods for treating alpha-1 antitrypsin deficiency ZA202007632B (en)

Applications Claiming Priority (1)

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US201662438219P 2016-12-22 2016-12-22

Publications (1)

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ZA202007632B true ZA202007632B (en) 2023-03-29

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ZA2020/07632A ZA202007632B (en) 2016-12-22 2020-12-08 Compositions and methods for treating alpha-1 antitrypsin deficiency

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EP (1) EP3559232A1 (enExample)
JP (2) JP7383478B2 (enExample)
KR (1) KR102551664B1 (enExample)
CN (2) CN117737062A (enExample)
AU (2) AU2017379073B2 (enExample)
BR (1) BR112019012825A2 (enExample)
CA (1) CA3047415A1 (enExample)
CO (1) CO2019007776A2 (enExample)
EA (1) EA201991455A1 (enExample)
IL (1) IL267448B2 (enExample)
MX (2) MX2019007594A (enExample)
MY (1) MY204487A (enExample)
PH (1) PH12019501457A1 (enExample)
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