TW202005978A - 新穎肝靶向腺相關病毒載體 - Google Patents

新穎肝靶向腺相關病毒載體 Download PDF

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TW202005978A
TW202005978A TW108116478A TW108116478A TW202005978A TW 202005978 A TW202005978 A TW 202005978A TW 108116478 A TW108116478 A TW 108116478A TW 108116478 A TW108116478 A TW 108116478A TW 202005978 A TW202005978 A TW 202005978A
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aav
seq
capsid
protein
sequence
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TW108116478A
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彼得 卡麥隆 克羅希
席薇亞 瑞米爾茲
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美商拜奧馬林製藥公司
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TW108116478A 2018-05-14 2019-05-13 新穎肝靶向腺相關病毒載體 TW202005978A (zh)

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US201862671265P 2018-05-14 2018-05-14
US62/671,265 2018-05-14

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KR20210008501A (ko) 2018-05-09 2021-01-22 바이오마린 파머수티컬 인크. 페닐케톤뇨증을 치료하는 방법
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CN116121274B (zh) * 2020-07-29 2024-11-19 北京三诺佳邑生物技术有限责任公司 一组肝靶向新型腺相关病毒的获得及其应用
KR20230078805A (ko) 2020-11-02 2023-06-02 바이오마린 파머수티컬 인크. 아데노-연관 바이러스의 농축 공정
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