KR20250023600A - 변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법 - Google Patents

변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법 Download PDF

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KR20250023600A
KR20250023600A KR1020257003821A KR20257003821A KR20250023600A KR 20250023600 A KR20250023600 A KR 20250023600A KR 1020257003821 A KR1020257003821 A KR 1020257003821A KR 20257003821 A KR20257003821 A KR 20257003821A KR 20250023600 A KR20250023600 A KR 20250023600A
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ser
glu
lys
ala
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데이비드 브이. 샤퍼
리 씨. 번
티모시 피. 데이
죤 지. 플래너리
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더 리젠츠 오브 더 유니버시티 오브 캘리포니아
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Publication of KR20250023600A publication Critical patent/KR20250023600A/ko
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KR1020257003821A 2017-06-30 2018-06-28 변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법 Pending KR20250023600A (ko)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201762527871P 2017-06-30 2017-06-30
US62/527,871 2017-06-30
US201762535042P 2017-07-20 2017-07-20
US62/535,042 2017-07-20
PCT/US2018/040115 WO2019006182A1 (en) 2017-06-30 2018-06-28 VIRIONS OF ADENO-ASSOCIATED VIRUSES OF CAPSID VARIANTS AND METHODS OF USE THEREOF
KR1020197027085A KR102766238B1 (ko) 2017-06-30 2018-06-28 변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법

Related Parent Applications (1)

Application Number Title Priority Date Filing Date
KR1020197027085A Division KR102766238B1 (ko) 2017-06-30 2018-06-28 변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법

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KR20250023600A true KR20250023600A (ko) 2025-02-18

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KR1020257003821A Pending KR20250023600A (ko) 2017-06-30 2018-06-28 변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법
KR1020197027085A Active KR102766238B1 (ko) 2017-06-30 2018-06-28 변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법

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US (2) US20200121746A1 (enExample)
EP (1) EP3645052A4 (enExample)
JP (2) JP7744659B2 (enExample)
KR (2) KR20250023600A (enExample)
CN (1) CN110461368A (enExample)
AU (2) AU2018290954B2 (enExample)
BR (1) BR112019019015A2 (enExample)
CA (1) CA3053154A1 (enExample)
MX (1) MX2019010910A (enExample)
WO (1) WO2019006182A1 (enExample)

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SMT202400520T1 (it) * 2011-04-22 2025-01-14 Univ California Virioni di virus adeno-associato con capside variante e relativi metodi di utilizzo
US10577627B2 (en) 2014-06-09 2020-03-03 Voyager Therapeutics, Inc. Chimeric capsids
WO2018187552A1 (en) 2017-04-05 2018-10-11 University Of Massachusetts Minigene therapy
CA3075656A1 (en) 2017-09-29 2019-04-04 Voyager Therapeutics, Inc. Rescue of central and peripheral neurological phenotype of friedreich's ataxia by intravenous delivery
WO2019158619A1 (en) * 2018-02-15 2019-08-22 Bjoerklund Tomas Modified viral capsids
US11821009B2 (en) 2018-05-15 2023-11-21 Cornell University Genetic modification of the AAV capsid resulting in altered tropism and enhanced vector delivery
CN113966399A (zh) 2018-09-26 2022-01-21 加州理工学院 用于靶向基因疗法的腺相关病毒组合物
AU2019346655B2 (en) 2018-09-28 2025-03-13 Voyager Therapeutics, Inc. Frataxin expression constructs having engineered promoters and methods of use thereof
TW202102526A (zh) * 2019-04-04 2021-01-16 美商銳進科斯生物股份有限公司 重組腺相關病毒及其用途
US12390539B2 (en) 2019-05-20 2025-08-19 University Of Massachusetts Minigene therapy
JP7791546B2 (ja) * 2019-10-31 2025-12-24 ウニベルジテート ベルン 眼遺伝子送達のためのａａｖベクター変異体
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