KR20220010062A - 리소좀 장애를 위한 유전자 요법 - Google Patents

리소좀 장애를 위한 유전자 요법 Download PDF

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KR20220010062A
KR20220010062A KR1020227000760A KR20227000760A KR20220010062A KR 20220010062 A KR20220010062 A KR 20220010062A KR 1020227000760 A KR1020227000760 A KR 1020227000760A KR 20227000760 A KR20227000760 A KR 20227000760A KR 20220010062 A KR20220010062 A KR 20220010062A
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nucleic acid
vector
raav
sequence
itr
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Korean (ko)
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아사 아벨리오비치
로라 헤크만
허브 린
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프리베일 테라퓨틱스, 인크.
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KR1020227000760A 2017-10-03 2018-10-03 리소좀 장애를 위한 유전자 요법 Ceased KR20220010062A (ko)

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Application Number Priority Date Filing Date Title
US201762567305P 2017-10-03 2017-10-03
US201762567303P 2017-10-03 2017-10-03
US62/567,303 2017-10-03
US62/567,305 2017-10-03
KR1020207012192A KR20200078513A (ko) 2017-10-03 2018-10-03 리소좀 장애를 위한 유전자 요법
PCT/US2018/054223 WO2019070891A1 (en) 2017-10-03 2018-10-03 GENE THERAPIES FOR LYSOSOMAL DISORDERS

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