KR20200078513A - 리소좀 장애를 위한 유전자 요법 - Google Patents

리소좀 장애를 위한 유전자 요법 Download PDF

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Publication number
KR20200078513A
KR20200078513A KR1020207012192A KR20207012192A KR20200078513A KR 20200078513 A KR20200078513 A KR 20200078513A KR 1020207012192 A KR1020207012192 A KR 1020207012192A KR 20207012192 A KR20207012192 A KR 20207012192A KR 20200078513 A KR20200078513 A KR 20200078513A
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nucleic acid
isolated nucleic
vector
sequence
itr
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Korean (ko)
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아사 아벨리오비치
로라 헤크만
허브 린
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프리베일 테라퓨틱스, 인크.
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Priority to KR1020227000760A priority Critical patent/KR20220010062A/ko
Publication of KR20200078513A publication Critical patent/KR20200078513A/ko
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KR1020207012192A 2017-10-03 2018-10-03 리소좀 장애를 위한 유전자 요법 Ceased KR20200078513A (ko)

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US201762567303P 2017-10-03 2017-10-03
US201762567305P 2017-10-03 2017-10-03
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PCT/US2018/054223 WO2019070891A1 (en) 2017-10-03 2018-10-03 GENE THERAPIES FOR LYSOSOMAL DISORDERS

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