KR20140011367A - 파브리 병을 치료하기 위한 투여 요법 - Google Patents
파브리 병을 치료하기 위한 투여 요법 Download PDFInfo
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- KR20140011367A KR20140011367A KR1020137026394A KR20137026394A KR20140011367A KR 20140011367 A KR20140011367 A KR 20140011367A KR 1020137026394 A KR1020137026394 A KR 1020137026394A KR 20137026394 A KR20137026394 A KR 20137026394A KR 20140011367 A KR20140011367 A KR 20140011367A
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- Prior art keywords
- gal
- agalsidase
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- deoxygalactonozirimycin
- patients
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| EP2252313B1 (en) | 2008-02-12 | 2015-04-08 | Amicus Therapeutics, Inc. | Method to predict response to pharmacological chaperone treatment of diseases |
| UY34317A (es) | 2011-09-12 | 2013-02-28 | Genzyme Corp | Anticuerpo antireceptor de célula T (alfa)/ß |
| US9790268B2 (en) | 2012-09-12 | 2017-10-17 | Genzyme Corporation | Fc containing polypeptides with altered glycosylation and reduced effector function |
| JP6588422B2 (ja) | 2013-03-11 | 2019-10-09 | ジェンザイム・コーポレーション | 糖類工学による部位特異的抗体−薬物コンジュゲーション |
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| US9675627B2 (en) * | 2014-04-14 | 2017-06-13 | Amicus Therapeutics, Inc. | Dosing regimens for treating and/or preventing cerebral amyloidoses |
| GB201508025D0 (en) * | 2015-05-11 | 2015-06-24 | Ucl Business Plc | Fabry disease gene therapy |
| WO2017027709A1 (en) | 2015-08-11 | 2017-02-16 | Cognoa, Inc. | Methods and apparatus to determine developmental progress with artificial intelligence and user input |
| US11972336B2 (en) | 2015-12-18 | 2024-04-30 | Cognoa, Inc. | Machine learning platform and system for data analysis |
| CN114159436A (zh) * | 2016-03-22 | 2022-03-11 | 阿米库斯治疗学公司 | 治疗在gla基因中具有g9331a突变的患者的法布里病的方法 |
| EP4378524A3 (en) * | 2016-07-19 | 2024-08-14 | Amicus Therapeutics, Inc. | Treatment of fabry disease in ert-naive and ert-experienced patients |
| CN110192252A (zh) | 2016-11-14 | 2019-08-30 | 科格诺亚公司 | 用于评估发育状况并提供覆盖度和可靠性控制的方法和装置 |
| EP3580700A4 (en) | 2017-02-09 | 2020-11-18 | Cognoa, Inc. | PLATFORM AND SYSTEM FOR DIGITAL PERSONALIZED MEDICINE |
| HUE065615T2 (hu) * | 2017-05-30 | 2024-06-28 | Amicus Therapeutics Inc | Migalasztát, vesekárosodással szövõdött Fabry-kórban szenvedõ betegeg kezelésére |
| KR20240017110A (ko) | 2017-05-30 | 2024-02-06 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 신장 손상을 갖는 파브리 환자를 치료하는 방법 |
| JP7066157B2 (ja) | 2017-06-14 | 2022-05-13 | 学校法人 明治薬科大学 | ファブリー病治療用医薬の組合せ物及びその利用 |
| EP3749307B1 (en) * | 2018-02-06 | 2025-12-10 | Amicus Therapeutics, Inc. | Use of migalastat for treating fabry disease in pregnant patients |
| AU2019326252A1 (en) * | 2018-08-20 | 2021-02-25 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having a mutation in the GLA gene |
| MX2021011493A (es) | 2019-03-22 | 2022-01-04 | Cognoa Inc | Métodos y dispositivos de terapia digital personalizados. |
| US12365734B2 (en) | 2019-04-03 | 2025-07-22 | Genzyme Corporation | Anti-alpha beta TCR binding polypeptides with reduced fragmentation |
| AU2020291002A1 (en) * | 2019-06-11 | 2022-01-06 | Amicus Therapeutics, Inc. | Methods of treating Fabry disease in patients having renal impairment |
| MX2022001623A (es) | 2019-08-07 | 2022-03-02 | Amicus Therapeutics Inc | Metodos para tratar la enfermedad de fabry en pacientes que tienen una mutacion en el gen gla. |
| US11623916B2 (en) | 2020-12-16 | 2023-04-11 | Amicus Therapeutics, Inc. | Highly purified batches of pharmaceutical grade migalastat and methods of producing the same |
| US20240120050A1 (en) * | 2022-10-07 | 2024-04-11 | Insight Direct Usa, Inc. | Machine learning method for predicting a health outcome of a patient using video and audio analytics |
| US20240197706A1 (en) * | 2022-12-13 | 2024-06-20 | Amicus Therapeutics, Inc. | Methods of improving the pharmacokinetics of migalastat |
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| EP2444102B1 (en) * | 2003-01-31 | 2015-04-08 | The Mount Sinai School of Medicine of New York University | Combination therapy for treating protein deficiency disorders |
| US7879354B2 (en) * | 2004-01-13 | 2011-02-01 | Mcneil-Ppc, Inc. | Rapidly disintegrating gelatinous coated tablets |
| CN100457106C (zh) * | 2005-06-15 | 2009-02-04 | 同济大学 | 1-脱氧野尻霉素在制备治疗糖尿病肾病药物中的应用 |
| PL2533050T6 (pl) * | 2006-05-16 | 2016-05-31 | Amicus Therapeutics Inc | Możliwości leczenia choroby Fabry'ego |
| EP2142197A4 (en) | 2007-03-30 | 2010-11-10 | Amicus Therapeutics Inc | PROCESS FOR THE TREATMENT OF FABRY DISEASE USING PHARMACOLOGICAL CHAPERONS |
| CA2685332A1 (en) * | 2007-04-26 | 2008-11-06 | Amicus Therapeutics, Inc. | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
| EP2185187A1 (en) * | 2007-08-29 | 2010-05-19 | Shire Human Genetic Therapies, Inc. | Subcutaneous administration of alpha-galatosidase a |
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