KR102000141B1 - 간상세포 유래 원추세포 생존능 인자를 인코딩하는 벡터 - Google Patents

간상세포 유래 원추세포 생존능 인자를 인코딩하는 벡터 Download PDF

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KR102000141B1
KR102000141B1 KR1020147011857A KR20147011857A KR102000141B1 KR 102000141 B1 KR102000141 B1 KR 102000141B1 KR 1020147011857 A KR1020147011857 A KR 1020147011857A KR 20147011857 A KR20147011857 A KR 20147011857A KR 102000141 B1 KR102000141 B1 KR 102000141B1
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rdcvf
nucleic acid
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KR20140092320A (ko
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티안치 루오
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웰스테이트 옵탈믹스 코퍼레이션
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KR1020147011857A 2011-10-27 2012-10-26 간상세포 유래 원추세포 생존능 인자를 인코딩하는 벡터 Active KR102000141B1 (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201161552155P 2011-10-27 2011-10-27
US61/552,155 2011-10-27
PCT/US2012/062106 WO2013063383A2 (en) 2011-10-27 2012-10-26 Vectors encoding rod-derived cone viability factor

Publications (2)

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KR20140092320A KR20140092320A (ko) 2014-07-23
KR102000141B1 true KR102000141B1 (ko) 2019-07-15

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US (2) US9265813B2 (cg-RX-API-DMAC7.html)
EP (1) EP2797613B1 (cg-RX-API-DMAC7.html)
JP (1) JP6293664B2 (cg-RX-API-DMAC7.html)
KR (1) KR102000141B1 (cg-RX-API-DMAC7.html)
CN (2) CN104321069A (cg-RX-API-DMAC7.html)
AU (1) AU2012321102C1 (cg-RX-API-DMAC7.html)
BR (1) BR112014010091B1 (cg-RX-API-DMAC7.html)
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US10004780B2 (en) * 2012-10-17 2018-06-26 INSERM (Institut National de la Santé et de la Recherche Médicale) Methods and pharmaceutical compositions for the treatment of age-related macular degeneration (AMD)
FI3851537T3 (fi) 2014-04-25 2024-03-21 Genethon Hyperbilirubinemian hoito
JP6684343B2 (ja) * 2015-05-21 2020-04-22 アンスティチュ ナショナル ドゥ ラ サンテ エ ドゥ ラ ルシェルシュ メディカル ニューロン生存因子の相乗組み合わせ及びその使用
GB201516066D0 (en) * 2015-09-10 2015-10-28 Young & Co Llp D Treatment of retinitis pigmentosa
JP7061067B2 (ja) 2015-12-14 2022-04-27 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア クリグラー・ナジャー症候群の処置のための組成物
US10857240B2 (en) 2016-01-05 2020-12-08 The Trustees Of The University Of Pennsylvania Methods and compositions for treatment of ocular disorders and blinding diseases
CN106148528B (zh) * 2016-07-11 2019-10-01 赵晨 一种遗传性Usher综合征的致病突变及其检测试剂
US10946063B2 (en) * 2016-10-11 2021-03-16 Welltat Ophthalmics Corporation Fusion protein between short form rod-derived cone viability factor and a hydrophilic peptide
KR102776626B1 (ko) * 2017-10-16 2025-03-04 비게네론 게엠베하 Aav 벡터
BR112020012471A2 (pt) * 2017-12-22 2020-11-24 Sparingvision construtos compreendendo fatores de viabilidade neuronal e usos dos mesmos
JP7213891B2 (ja) * 2018-01-30 2023-01-27 ユニベルシテイト ゲント 白内障を処置するのに使用するための組成物
CN108504685A (zh) * 2018-03-27 2018-09-07 宜明细胞生物科技有限公司 一种利用CRISPR/Cas9系统同源重组修复IL-2RG缺陷基因的方法
SG11202102140WA (en) * 2018-09-07 2021-04-29 Univ Southern California Cryopreservation of cell-seeded substrates and related methods
KR20210092755A (ko) * 2018-11-14 2021-07-26 리젠엑스바이오 인크. 신경원성 세로이드 리포푸신증에 대한 유전자 요법
PE20211342A1 (es) * 2018-12-19 2021-07-26 Versameb Ag Acido ribonucleico (arn) que codifica para una proteina
CN114651003A (zh) 2019-09-10 2022-06-21 黑曜石疗法公司 用于可调调节的ca2-il15融合蛋白
EP4074828A4 (en) * 2019-12-09 2023-12-27 Chigenovo Co., Ltd. Uses of cyp4v2 and rdcvf in preparation of drugs
CN111733174B (zh) * 2020-08-07 2021-02-09 北京大学第三医院（北京大学第三临床医学院） 一种分离的核酸分子及其用途
KR20230092880A (ko) * 2020-08-28 2023-06-26 조인트 스탁 컴퍼니 "바이오케드" AAV5-기반의 SARS-CoV-2 백신
WO2024206928A1 (en) 2023-03-30 2024-10-03 Pharma Cinq, Llc VECTOR ENCODING ROD-DERIVED CONE VIABILITY FACTOR AND HUMAN IgK SIGNAL SEQUENCE

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