JP7327803B2 - 筋萎縮性側索硬化症(als)を処置する方法 - Google Patents
筋萎縮性側索硬化症(als)を処置する方法 Download PDFInfo
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| US10781453B2 (en) | 2016-09-30 | 2020-09-22 | Regeneron Pharmaceuticals, Inc. | Non-human animals having a hexanucleotide repeat expansion in a C9ORF72 locus |
| CN111448321A (zh) | 2017-09-22 | 2020-07-24 | 马萨诸塞大学 | Sod1双表达载体及其用途 |
| KR20210105914A (ko) | 2018-12-20 | 2021-08-27 | 리제너론 파마슈티칼스 인코포레이티드 | 뉴클레아제-매개 반복부 팽창 |
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| CA3172178A1 (en) * | 2020-03-18 | 2021-09-23 | Benjamin OAKES | Compositions and methods for the targeting of c9orf72 |
| US20220290136A1 (en) * | 2020-09-30 | 2022-09-15 | Crispr Therapeutics Ag | Materials and methods for treatment of amyotrophic lateral sclerosis |
| GB202105455D0 (en) * | 2021-04-16 | 2021-06-02 | Ucl Business Ltd | Composition |
| WO2023025103A1 (en) * | 2021-08-22 | 2023-03-02 | Huigene Therapeutics Co., Ltd. | Crispr-cas13 system for treating sod1-associated diseases |
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| EP3622073A1 (en) | 2020-03-18 |
| AU2018264996A1 (en) | 2019-12-05 |
| US11859179B2 (en) | 2024-01-02 |
| EP3622073A4 (en) | 2021-01-06 |
| JP2020519284A (ja) | 2020-07-02 |
| US20200354716A1 (en) | 2020-11-12 |
| WO2018208972A1 (en) | 2018-11-15 |
| US20240167025A1 (en) | 2024-05-23 |
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