JP6929865B2 - 角膜ジストロフィーの治療方法 - Google Patents

角膜ジストロフィーの治療方法 Download PDF

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JP6929865B2
JP6929865B2 JP2018545108A JP2018545108A JP6929865B2 JP 6929865 B2 JP6929865 B2 JP 6929865B2 JP 2018545108 A JP2018545108 A JP 2018545108A JP 2018545108 A JP2018545108 A JP 2018545108A JP 6929865 B2 JP6929865 B2 JP 6929865B2
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nucleic acid
certain embodiments
corneal
stem cells
target nucleic
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JP2018534114A5 (enExample
JP2018534114A (ja
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アンドリュー ネスビット
アンドリュー ネスビット
ジーン リー
ジーン リー
スン−ヨン チョ
スン−ヨン チョ
ラリー デディオニシオ
ラリー デディオニシオ
タラ ムーア
タラ ムーア
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Avellino Lab USA Inc
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JP2018545108A 2015-11-13 2016-11-14 角膜ジストロフィーの治療方法 Expired - Fee Related JP6929865B2 (ja)

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US201562255310P 2015-11-13 2015-11-13
US62/255,310 2015-11-13
PCT/US2016/061893 WO2017083852A1 (en) 2015-11-13 2016-11-14 Methods for the treatment of corneal dystrophies

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EP (2) EP3374502B1 (enExample)
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CN (1) CN108699542A (enExample)
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JP2021506251A (ja) 2017-12-14 2021-02-22 クリスパー セラピューティクス アーゲー 新規ｒｎａプログラム可能エンドヌクレアーゼ系、ならびにゲノム編集および他の適用におけるその使用
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