JP6909212B2 - 肝臓特異的コンストラクト、第ｖｉｉｉ因子発現カセット、およびその使用の方法 - Google Patents

肝臓特異的コンストラクト、第ｖｉｉｉ因子発現カセット、およびその使用の方法 Download PDF

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JP6909212B2
JP6909212B2 JP2018521965A JP2018521965A JP6909212B2 JP 6909212 B2 JP6909212 B2 JP 6909212B2 JP 2018521965 A JP2018521965 A JP 2018521965A JP 2018521965 A JP2018521965 A JP 2018521965A JP 6909212 B2 JP6909212 B2 JP 6909212B2
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sequence
hfviii
seq
transgene
expression construct
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JP2018531614A5 (enExample
JP2018531614A (ja
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ブリジット イー． ライリー，
ブリジット イー． ライリー，
ゲイリー ケー． リー，
ゲイリー ケー． リー，
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Sangamo Therapeutics Inc
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JP2018521965A 2015-10-28 2016-07-13 肝臓特異的コンストラクト、第ｖｉｉｉ因子発現カセット、およびその使用の方法 Active JP6909212B2 (ja)

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US201562247469P 2015-10-28 2015-10-28
US62/247,469 2015-10-28
US201662307897P 2016-03-14 2016-03-14
US62/307,897 2016-03-14
US201662315438P 2016-03-30 2016-03-30
US62/315,438 2016-03-30
US201662326229P 2016-04-22 2016-04-22
US62/326,229 2016-04-22
US201662355106P 2016-06-27 2016-06-27
US62/355,106 2016-06-27
PCT/US2016/042099 WO2017074526A1 (en) 2015-10-28 2016-07-13 Liver-specific constructs, factor viii expression cassettes and methods of use thereof

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CN (2) CN115141836B (enExample)
AU (1) AU2016343887B2 (enExample)
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