AU2016343887B2 - Liver-specific constructs, factor VIII expression cassettes and methods of use thereof - Google Patents

Liver-specific constructs, factor VIII expression cassettes and methods of use thereof Download PDF

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AU2016343887B2
AU2016343887B2 AU2016343887A AU2016343887A AU2016343887B2 AU 2016343887 B2 AU2016343887 B2 AU 2016343887B2 AU 2016343887 A AU2016343887 A AU 2016343887A AU 2016343887 A AU2016343887 A AU 2016343887A AU 2016343887 B2 AU2016343887 B2 AU 2016343887B2
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sequence
transgene
seq
protein
expression construct
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AU2016343887A1 (en
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Gary K. Lee
Brigit E. RILEY
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Sangamo Therapeutics Inc
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Sangamo Therapeutics Inc
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    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79—Vectors or expression systems specially adapted for eukaryotic hosts
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AU2016343887A 2015-10-28 2016-07-13 Liver-specific constructs, factor VIII expression cassettes and methods of use thereof Active AU2016343887B2 (en)

Applications Claiming Priority (11)

Application Number Priority Date Filing Date Title
US201562247469P 2015-10-28 2015-10-28
US62/247,469 2015-10-28
US201662307897P 2016-03-14 2016-03-14
US62/307,897 2016-03-14
US201662315438P 2016-03-30 2016-03-30
US62/315,438 2016-03-30
US201662326229P 2016-04-22 2016-04-22
US62/326,229 2016-04-22
US201662355106P 2016-06-27 2016-06-27
US62/355,106 2016-06-27
PCT/US2016/042099 WO2017074526A1 (en) 2015-10-28 2016-07-13 Liver-specific constructs, factor viii expression cassettes and methods of use thereof

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AU2016343887A1 AU2016343887A1 (en) 2018-05-10
AU2016343887B2 true AU2016343887B2 (en) 2023-04-06

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KR (2) KR102766526B1 (enExample)
CN (2) CN115141836B (enExample)
AU (1) AU2016343887B2 (enExample)
CA (1) CA3002524A1 (enExample)
CO (1) CO2018005215A2 (enExample)
IL (1) IL258826B2 (enExample)
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