JP6224459B2 - 組織特異性を改変し、ａａｖ９媒介遺伝子導入を改善するための組成物および方法 - Google Patents

組織特異性を改変し、ａａｖ９媒介遺伝子導入を改善するための組成物および方法 Download PDF

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JP6224459B2
JP6224459B2 JP2013554622A JP2013554622A JP6224459B2 JP 6224459 B2 JP6224459 B2 JP 6224459B2 JP 2013554622 A JP2013554622 A JP 2013554622A JP 2013554622 A JP2013554622 A JP 2013554622A JP 6224459 B2 JP6224459 B2 JP 6224459B2
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aav9
aav
galactose
vector
binding
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JP2014507154A (ja
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ウイルソン，ジエイムズ・エム
ベル，クリステイー・エル
バンデンバーグ，リユク・エイチ
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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JP2013554622A 2011-02-17 2012-02-17 組織特異性を改変し、ａａｖ９媒介遺伝子導入を改善するための組成物および方法 Expired - Fee Related JP6224459B2 (ja)

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US201161443879P 2011-02-17 2011-02-17
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PCT/US2012/025550 WO2012112832A1 (en) 2011-02-17 2012-02-17 Compositions and methods for altering tissue specificity and improving aav9-mediated gene transfer

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