JP2025521102A5 - - Google Patents

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Publication number
JP2025521102A5
JP2025521102A5 JP2024566858A JP2024566858A JP2025521102A5 JP 2025521102 A5 JP2025521102 A5 JP 2025521102A5 JP 2024566858 A JP2024566858 A JP 2024566858A JP 2024566858 A JP2024566858 A JP 2024566858A JP 2025521102 A5 JP2025521102 A5 JP 2025521102A5
Authority
JP
Japan
Prior art keywords
nucleic acid
sequence
seq
molecule according
splicing
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024566858A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025521102A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/066969 external-priority patent/WO2023220742A2/en
Publication of JP2025521102A publication Critical patent/JP2025521102A/ja
Publication of JP2025521102A5 publication Critical patent/JP2025521102A5/ja
Pending legal-status Critical Current

Links

JP2024566858A 2022-05-13 2023-05-12 Ａｂｃａ４トランススプライシング分子 Pending JP2025521102A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263341665P 2022-05-13 2022-05-13
US63/341,665 2022-05-13
US202363478472P 2023-01-04 2023-01-04
US63/478,472 2023-01-04
PCT/US2023/066969 WO2023220742A2 (en) 2022-05-13 2023-05-12 Abca4 trans-splicing molecules

Publications (2)

Publication Number Publication Date
JP2025521102A JP2025521102A (ja) 2025-07-08
JP2025521102A5 true JP2025521102A5 (enExample) 2026-05-19

Family

ID=88731152

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024566858A Pending JP2025521102A (ja) 2022-05-13 2023-05-12 Ａｂｃａ４トランススプライシング分子

Country Status (11)

Country Link
US (3) US20240042057A1 (enExample)
EP (1) EP4522758A4 (enExample)
JP (1) JP2025521102A (enExample)
KR (1) KR20250011939A (enExample)
CN (1) CN119731328A (enExample)
AU (1) AU2023269865A1 (enExample)
CA (1) CA3252043A1 (enExample)
GB (1) GB2634434A (enExample)
IL (1) IL316944A (enExample)
MX (1) MX2024014029A (enExample)
WO (1) WO2023220742A2 (enExample)

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MX2020010959A (es) 2018-04-17 2021-01-15 Univ Pennsylvania Moleculas de empalme trans.
IL316944A (en) 2022-05-13 2025-01-01 Ascidian Therapeutics Inc ABCA4 cross-linking molecules
WO2025217163A2 (en) 2024-04-08 2025-10-16 The Broad Institute, Inc. Novel aav capsids binding to human cd59
WO2025217174A1 (en) 2024-04-08 2025-10-16 The Broad Institute, Inc. Aav capsid modifications that enable improved cns-wide gene delivery through interactions with carbonic anhydrase iv

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