JP2024507717A5 - - Google Patents

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Publication number
JP2024507717A5
JP2024507717A5 JP2023547237A JP2023547237A JP2024507717A5 JP 2024507717 A5 JP2024507717 A5 JP 2024507717A5 JP 2023547237 A JP2023547237 A JP 2023547237A JP 2023547237 A JP2023547237 A JP 2023547237A JP 2024507717 A5 JP2024507717 A5 JP 2024507717A5
Authority
JP
Japan
Prior art keywords
nucleotides
premrna
item
approximately
nucleic acid
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023547237A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024507717A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/015074 external-priority patent/WO2022169947A2/en
Publication of JP2024507717A publication Critical patent/JP2024507717A/ja
Publication of JP2024507717A5 publication Critical patent/JP2024507717A5/ja
Pending legal-status Critical Current

Links

JP2023547237A 2021-02-03 2022-02-03 ポリシスチン発現に関連する状態及び疾患の治療のための組成物 Pending JP2024507717A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163145288P 2021-02-03 2021-02-03
US63/145,288 2021-02-03
PCT/US2022/015074 WO2022169947A2 (en) 2021-02-03 2022-02-03 Compositions for treatment of conditions and diseases associated with polycystin expression

Publications (2)

Publication Number Publication Date
JP2024507717A JP2024507717A (ja) 2024-02-21
JP2024507717A5 true JP2024507717A5 (https=) 2025-02-12

Family

ID=82741748

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023547237A Pending JP2024507717A (ja) 2021-02-03 2022-02-03 ポリシスチン発現に関連する状態及び疾患の治療のための組成物

Country Status (12)

Country Link
US (1) US20240117353A1 (https=)
EP (1) EP4288543A4 (https=)
JP (1) JP2024507717A (https=)
KR (1) KR20230150973A (https=)
CN (1) CN117413061A (https=)
AR (1) AR124809A1 (https=)
AU (1) AU2022215577A1 (https=)
BR (1) BR112023015636A2 (https=)
CA (1) CA3207341A1 (https=)
MX (1) MX2023009151A (https=)
TW (1) TW202242113A (https=)
WO (1) WO2022169947A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4612295A1 (en) * 2022-10-31 2025-09-10 Stoke Therapeutics, Inc. Antisense oligomers for treatment of non-sense mediated rna decay based conditions and diseases

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6916619B2 (en) * 2001-10-12 2005-07-12 Athena Diagnostics, Inc. Compositions and methods for genetic analysis of polycystic kidney disease
US11096956B2 (en) * 2015-12-14 2021-08-24 Stoke Therapeutics, Inc. Antisense oligomers and uses thereof
JP2018538287A (ja) * 2015-12-14 2018-12-27 コールド スプリング ハーバー ラボラトリー 多発性嚢胞腎の処置のためのアンチセンスオリゴマー
HUE070436T2 (hu) * 2017-10-23 2025-06-28 Stoke Therapeutics Inc Antiszensz oligomerek nonszensz-mediált RNS-lebomláson alapuló állapotok és betegségek kezelésére

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