JP2022544702A5 - - Google Patents
Info
- Publication number
- JP2022544702A5 JP2022544702A5 JP2022511203A JP2022511203A JP2022544702A5 JP 2022544702 A5 JP2022544702 A5 JP 2022544702A5 JP 2022511203 A JP2022511203 A JP 2022511203A JP 2022511203 A JP2022511203 A JP 2022511203A JP 2022544702 A5 JP2022544702 A5 JP 2022544702A5
- Authority
- JP
- Japan
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962888887P | 2019-08-19 | 2019-08-19 | |
| US62/888,887 | 2019-08-19 | ||
| US202063049262P | 2020-07-08 | 2020-07-08 | |
| US63/049,262 | 2020-07-08 | ||
| PCT/US2020/047081 WO2021034985A1 (en) | 2019-08-19 | 2020-08-19 | Compositions and methods for modulating splicing and protein expression |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022544702A JP2022544702A (ja) | 2022-10-20 |
| JPWO2021034985A5 JPWO2021034985A5 (https=) | 2023-08-28 |
| JP2022544702A5 true JP2022544702A5 (https=) | 2023-08-28 |
Family
ID=74659533
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022511203A Pending JP2022544702A (ja) | 2019-08-19 | 2020-08-19 | スプライシングおよびタンパク質発現を調節するための組成物および方法 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20220290142A1 (https=) |
| EP (1) | EP4017979A4 (https=) |
| JP (1) | JP2022544702A (https=) |
| KR (1) | KR20220104677A (https=) |
| CN (1) | CN114746550A (https=) |
| AU (1) | AU2020334067A1 (https=) |
| BR (1) | BR112022002905A2 (https=) |
| CA (1) | CA3147970A1 (https=) |
| IL (1) | IL290595A (https=) |
| MX (1) | MX2022002198A (https=) |
| WO (1) | WO2021034985A1 (https=) |
Families Citing this family (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2020237294A1 (en) * | 2019-05-27 | 2020-12-03 | Murdoch University | Novel retinitis pigmentosa treatment |
| EP4025345A4 (en) * | 2019-09-03 | 2024-02-28 | The Regents Of The University Of Colorado, A Body Corporate | Systems, methods, and compositions for the rapid early-detection of host rna biomarkers of infection and early identification of covid-19 coronavirus infection in humans |
| AU2021272832A1 (en) * | 2020-05-11 | 2022-12-15 | The Florey Institute Of Neuroscience And Mental Health | Compositions and methods for treating disorders associated with loss-of-function mutations in SYNGAP1 |
| EP4359538A4 (en) * | 2021-06-21 | 2025-09-17 | Stoke Therapeutics Inc | ANTISENSE OLIGOMERS FOR THE TREATMENT OF CONDITIONS AND DISEASES BASED ON THE DEGRADATION OF NONSENSE MRNA |
| WO2023004021A2 (en) * | 2021-07-23 | 2023-01-26 | The Children's Medical Center Corporation | Zinc finger ccch-type containing 14 (zc3h14) mutants and methods of use |
| WO2023163801A1 (en) * | 2022-02-24 | 2023-08-31 | Q-State Biosciences, Inc. | Therapeutics for syngap haploinsufficiency |
| US20250230467A1 (en) * | 2022-04-05 | 2025-07-17 | The Johns Hopkins University | Methods and materials for treating syngap1-associated neurodevelopmental disorders |
| WO2023212625A1 (en) * | 2022-04-28 | 2023-11-02 | AcuraStem Incorporated | Syf2 antisense oligonucleotides |
| WO2023220727A1 (en) * | 2022-05-13 | 2023-11-16 | The Trustees Of The University Of Pennsylvania | Compositions for treating syngap-1 related neurodevelopmental disorders |
| CN119948160A (zh) * | 2022-06-28 | 2025-05-06 | 新加坡科技研究局 | 寡核苷酸 |
| WO2025090633A1 (en) * | 2023-10-23 | 2025-05-01 | Regeneron Pharmaceuticals, Inc. | Compositions and methods comprising small nuclear rna (snrna) for treating genetic epilepsies |
| WO2025111249A2 (en) * | 2023-11-20 | 2025-05-30 | Dana-Farber Cancer Institute, Inc. | Methods, kits and systems for determining sarcomatoid differentiation of renal cell carcinoma and methods for treating based on the same |
| GB202401412D0 (en) * | 2024-02-02 | 2024-03-20 | Harness Therapeutics Ltd | Functional nucleic acid |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2009064920A2 (en) * | 2007-11-13 | 2009-05-22 | Isis Pharmaceuticals, Inc. | Compounds and methods for modulating protein expression |
| JP2012507989A (ja) * | 2008-11-07 | 2012-04-05 | センター ホスピタライヤー ユニヴェルシテール サント−ジュスティーヌ | Ｓｙｎｇａｐ１機能不全ならびに精神遅滞の診断および治療用途でのその使用 |
| CN107109411B (zh) * | 2014-10-03 | 2022-07-01 | 冷泉港实验室 | 核基因输出的定向增加 |
| EP3359685B1 (en) * | 2015-10-09 | 2026-01-28 | University Of Southampton | Modulation of gene expression for deregulated protein expression |
| JP2018538287A (ja) * | 2015-12-14 | 2018-12-27 | コールド スプリング ハーバー ラボラトリー | 多発性嚢胞腎の処置のためのアンチセンスオリゴマー |
| WO2017106375A1 (en) * | 2015-12-14 | 2017-06-22 | Cold Spring Harbor Laboratory | Antisense oligomers for treatment of tuberous sclerosis complex |
| EP3390666A4 (en) * | 2015-12-14 | 2019-08-07 | Cold Spring Harbor Laboratory | COMPOSITIONS AND METHODS OF TREATING NURSE DISEASES |
| CA3005090A1 (en) * | 2015-12-14 | 2017-06-22 | Cold Spring Harbor Laboratory | Compositions and methods for treatment of liver diseases |
| EP3933041B1 (en) * | 2015-12-14 | 2024-01-31 | Cold Spring Harbor Laboratory | Antisense oligomers for treatment of autosomal dominant retardation |
| EP3390634A4 (en) * | 2015-12-14 | 2019-08-14 | Cold Spring Harbor Laboratory | COMPOSITIONS AND METHODS FOR THE TREATMENT OF EYE DISEASES |
| JP2019535789A (ja) * | 2016-11-28 | 2019-12-12 | ピーティーシー セラピューティクス，インコーポレーテッド | Ｒｎａスプライシングを調節する方法 |
| SG11202001590RA (en) * | 2017-08-25 | 2020-03-30 | Stoke Therapeutics Inc | Antisense oligomers for treatment of conditions and diseases |
| GB2610100B (en) * | 2017-10-23 | 2023-08-16 | Stoke Therapeutics Inc | Antisense oligomers for treatment of non-sense mediated RNA decay based conditions and diseases |
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2020
- 2020-08-19 EP EP20855637.3A patent/EP4017979A4/en active Pending
- 2020-08-19 CN CN202080073358.0A patent/CN114746550A/zh active Pending
- 2020-08-19 AU AU2020334067A patent/AU2020334067A1/en active Pending
- 2020-08-19 KR KR1020227008965A patent/KR20220104677A/ko active Pending
- 2020-08-19 JP JP2022511203A patent/JP2022544702A/ja active Pending
- 2020-08-19 MX MX2022002198A patent/MX2022002198A/es unknown
- 2020-08-19 BR BR112022002905A patent/BR112022002905A2/pt unknown
- 2020-08-19 CA CA3147970A patent/CA3147970A1/en active Pending
- 2020-08-19 WO PCT/US2020/047081 patent/WO2021034985A1/en not_active Ceased
-
2022
- 2022-02-13 IL IL290595A patent/IL290595A/en unknown
- 2022-02-16 US US17/673,226 patent/US20220290142A1/en active Pending