JP2024505197A5 - - Google Patents

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Publication number
JP2024505197A5
JP2024505197A5 JP2023544528A JP2023544528A JP2024505197A5 JP 2024505197 A5 JP2024505197 A5 JP 2024505197A5 JP 2023544528 A JP2023544528 A JP 2023544528A JP 2023544528 A JP2023544528 A JP 2023544528A JP 2024505197 A5 JP2024505197 A5 JP 2024505197A5
Authority
JP
Japan
Prior art keywords
neuron
composition
ligand
item
vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023544528A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024505197A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/013658 external-priority patent/WO2022159871A1/en
Publication of JP2024505197A publication Critical patent/JP2024505197A/ja
Publication of JP2024505197A5 publication Critical patent/JP2024505197A5/ja
Pending legal-status Critical Current

Links

JP2023544528A 2021-01-25 2022-01-25 焦点てんかんおよび神経因性疼痛を処置するためのアデノ随伴ウイルスカプシドおよび操作されたリガンド依存性イオンチャネル Pending JP2024505197A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202163141121P 2021-01-25 2021-01-25
US202163141124P 2021-01-25 2021-01-25
US63/141,124 2021-01-25
US63/141,121 2021-01-25
US202163285929P 2021-12-03 2021-12-03
US63/285,929 2021-12-03
PCT/US2022/013658 WO2022159871A1 (en) 2021-01-25 2022-01-25 Adeno-associated virus capsids and engineered ligand-gated ion channels for treating focal epilepsy and neuropathic pain

Publications (2)

Publication Number Publication Date
JP2024505197A JP2024505197A (ja) 2024-02-05
JP2024505197A5 true JP2024505197A5 (https=) 2025-02-03

Family

ID=82549286

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023544528A Pending JP2024505197A (ja) 2021-01-25 2022-01-25 焦点てんかんおよび神経因性疼痛を処置するためのアデノ随伴ウイルスカプシドおよび操作されたリガンド依存性イオンチャネル

Country Status (9)

Country Link
US (1) US20240108760A1 (https=)
EP (1) EP4281551A4 (https=)
JP (1) JP2024505197A (https=)
KR (1) KR20230149299A (https=)
AU (1) AU2022211055A1 (https=)
CA (1) CA3205877A1 (https=)
IL (1) IL304511A (https=)
MX (1) MX2023008738A (https=)
WO (1) WO2022159871A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025188847A1 (en) * 2024-03-07 2025-09-12 The Texas A&M University System Method for treating epilepsy
WO2025230969A1 (en) * 2024-05-02 2025-11-06 4D Molecular Therapeutics Inc. Aav variants with improved cns tropism and uses thereof

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2345731B1 (en) * 2003-09-30 2015-10-21 The Trustees of the University of Pennsylvania Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof
US20170007720A1 (en) * 2014-02-21 2017-01-12 University Of Florida Research Foundation, Inc. Methods and compositions for gene delivery to on bipolar cells
AU2016324317A1 (en) * 2015-09-17 2018-03-08 Coda Biotherapeutics, Inc. Compositions and methods for treating neurological disorders
WO2017214442A1 (en) * 2016-06-08 2017-12-14 President And Fellows Of Harvard College Methods and compositions for reducing tactile dysfunction and anxiety associated with autism spectrum disorder, rett syndrome, and fragile x syndrome
US10538571B2 (en) * 2017-11-27 2020-01-21 Coda Biotherapeutics, Inc. Compositions and methods for neurological diseases
EP3810775A1 (en) * 2018-06-21 2021-04-28 The Board Of Regents Of The University Of Texas System Correction of dystrophin exon 43, exon 45, or exon 52 deletions in duchenne muscular dystrophy

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