JP2022533451A5 - - Google Patents

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Publication number
JP2022533451A5
JP2022533451A5 JP2021569550A JP2021569550A JP2022533451A5 JP 2022533451 A5 JP2022533451 A5 JP 2022533451A5 JP 2021569550 A JP2021569550 A JP 2021569550A JP 2021569550 A JP2021569550 A JP 2021569550A JP 2022533451 A5 JP2022533451 A5 JP 2022533451A5
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Japan
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composition according
psen1
disease
promoter
human
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JP2021569550A
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Japanese (ja)
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JP7686573B2 (ja
JP7686573B6 (ja
JP2022533451A (ja
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Priority claimed from PCT/US2020/034040 external-priority patent/WO2020242892A1/en
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Publication of JP2022533451A5 publication Critical patent/JP2022533451A5/ja
Publication of JP7686573B2 publication Critical patent/JP7686573B2/ja
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Publication of JP7686573B6 publication Critical patent/JP7686573B6/ja
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JP2021569550A 2019-05-24 2020-05-21 アルツハイマー病のための遺伝子治療 Active JP7686573B6 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962852716P 2019-05-24 2019-05-24
US62/852,716 2019-05-24
PCT/US2020/034040 WO2020242892A1 (en) 2019-05-24 2020-05-21 Gene therapy for alzheimer's disease

Publications (4)

Publication Number Publication Date
JP2022533451A JP2022533451A (ja) 2022-07-22
JP2022533451A5 true JP2022533451A5 (https=) 2023-05-30
JP7686573B2 JP7686573B2 (ja) 2025-06-02
JP7686573B6 JP7686573B6 (ja) 2025-07-04

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ID=73553511

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JP2021569550A Active JP7686573B6 (ja) 2019-05-24 2020-05-21 アルツハイマー病のための遺伝子治療

Country Status (8)

Country Link
US (1) US12540334B2 (https=)
EP (1) EP3976637A4 (https=)
JP (1) JP7686573B6 (https=)
CN (1) CN114144425B (https=)
AU (1) AU2020285638A1 (https=)
CA (1) CA3141712A1 (https=)
IL (1) IL288266A (https=)
WO (1) WO2020242892A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
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AU2023312939A1 (en) * 2022-07-25 2025-03-06 Katholieke Universiteit Leuven Antisense oligonucleotides for treating a disease or condition associated with an abnormal processing of app

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