JP2023126658A5 - - Google Patents
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- Publication number
- JP2023126658A5 JP2023126658A5 JP2023119196A JP2023119196A JP2023126658A5 JP 2023126658 A5 JP2023126658 A5 JP 2023126658A5 JP 2023119196 A JP2023119196 A JP 2023119196A JP 2023119196 A JP2023119196 A JP 2023119196A JP 2023126658 A5 JP2023126658 A5 JP 2023126658A5
- Authority
- JP
- Japan
- Prior art keywords
- agents
- transgene
- medicament
- administration
- raav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (8)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962833979P | 2019-04-15 | 2019-04-15 | |
| US62/833,979 | 2019-04-15 | ||
| US201962926317P | 2019-10-25 | 2019-10-25 | |
| US62/926,317 | 2019-10-25 | ||
| US202062967219P | 2020-01-29 | 2020-01-29 | |
| US62/967,219 | 2020-01-29 | ||
| PCT/US2020/028269 WO2020214672A1 (en) | 2019-04-15 | 2020-04-15 | Methods and compositions for transgene expression |
| JP2021561893A JP2022529470A (ja) | 2019-04-15 | 2020-04-15 | 導入遺伝子発現のための方法及び組成物 |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021561893A Division JP2022529470A (ja) | 2019-04-15 | 2020-04-15 | 導入遺伝子発現のための方法及び組成物 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023126658A JP2023126658A (ja) | 2023-09-07 |
| JP2023126658A5 true JP2023126658A5 (https=) | 2023-10-24 |
Family
ID=70779846
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021561893A Pending JP2022529470A (ja) | 2019-04-15 | 2020-04-15 | 導入遺伝子発現のための方法及び組成物 |
| JP2023119196A Pending JP2023126658A (ja) | 2019-04-15 | 2023-07-21 | 導入遺伝子発現のための方法及び組成物 |
Family Applications Before (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021561893A Pending JP2022529470A (ja) | 2019-04-15 | 2020-04-15 | 導入遺伝子発現のための方法及び組成物 |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20220195461A1 (https=) |
| EP (1) | EP3955970A1 (https=) |
| JP (2) | JP2022529470A (https=) |
| KR (1) | KR20220047538A (https=) |
| CN (1) | CN114340683A (https=) |
| AU (1) | AU2020257182A1 (https=) |
| BR (1) | BR112021020706A2 (https=) |
| CA (1) | CA3137078A1 (https=) |
| IL (1) | IL287262A (https=) |
| MX (1) | MX2021012682A (https=) |
| PH (1) | PH12021552609A1 (https=) |
| SG (1) | SG11202111353QA (https=) |
| WO (1) | WO2020214672A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2017139381A1 (en) | 2016-02-08 | 2017-08-17 | University Of Iowa Research Foundation | Methods to produce chimeric adeno-associated virus/bocavirus parvovirus |
| CA3198936A1 (en) | 2016-03-07 | 2017-09-14 | University Of Iowa Research Foundation | Aav-mediated expression using a synthetic promoter and enhancer |
| US12173305B2 (en) | 2016-05-26 | 2024-12-24 | University Of Iowa Research Foundation | cis and trans requirements for terminal resolution of human bocavirus 1 |
| US11142775B2 (en) | 2017-01-13 | 2021-10-12 | University Of Iowa Research Foundation | Bocaparvovirus small noncoding RNA and uses thereof |
| US20220241436A1 (en) * | 2019-04-15 | 2022-08-04 | University Of Iowa Research Foundation | Compositions and methods for treatment of cystic fibrosis |
Family Cites Families (20)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5478745A (en) | 1992-12-04 | 1995-12-26 | University Of Pittsburgh | Recombinant viral vector system |
| PT728214E (pt) | 1993-11-09 | 2004-11-30 | Ohio Med College | Linhas celulares estaveis capazes de expressar o gene de replicacao do virus adeno-associado |
| PT733103E (pt) | 1993-11-09 | 2004-07-30 | Targeted Genetics Corp | Criacao de elevados titulos de vectores de aav recombinantes |
| AU707866B2 (en) | 1994-12-06 | 1999-07-22 | Targeted Genetics Corporation | Packaging cell lines for generation of high titers of recombinant AAV vectors |
| US5656785A (en) | 1995-08-07 | 1997-08-12 | The Charles Stark Draper Laboratory, Inc. | Micromechanical contact load force sensor for sensing magnitude and distribution of loads and tool employing micromechanical contact load force sensor |
| AU5445998A (en) | 1996-11-19 | 1998-06-10 | Surgx Corporation | A transient voltage protection device and method of making same |
| AU741605B2 (en) | 1996-12-18 | 2001-12-06 | Targeted Genetics Corporation | AAV split-packaging genes and cell lines comprising such genes for use in the production of recombinant AAV vectors |
| JP2007524379A (ja) * | 2003-03-31 | 2007-08-30 | ユニバーシテイ・オブ・アイオワ・リサーチ・フアウンデーシヨン | 上皮ナトリウムチャンネル関連障害のＰｈａｒｍｉｃｏ−遺伝子治療 |
| US9233131B2 (en) | 2003-06-30 | 2016-01-12 | The Regents Of The University Of California | Mutant adeno-associated virus virions and methods of use thereof |
| CA2788682C (en) * | 2010-02-05 | 2019-03-05 | The University Of North Carolina At Chapel Hill | Compositions and methods for enhanced parvovirus transduction |
| KR20210122917A (ko) * | 2013-03-14 | 2021-10-12 | 샤이어 휴먼 지네틱 테라피즈 인크. | Cftr mrna 조성물 및 관련 방법 및 사용 |
| AU2014251099B2 (en) * | 2013-04-08 | 2019-01-17 | The University Of Kansas | Chimeric adeno-associated virus/ bocavirus parvovirus vector |
| KR102537394B1 (ko) * | 2014-03-17 | 2023-05-30 | 애드베룸 바이오테크놀로지스, 인코포레이티드 | 원추세포에서 증강된 유전자 발현을 위한 조성물 및 방법 |
| WO2017139381A1 (en) * | 2016-02-08 | 2017-08-17 | University Of Iowa Research Foundation | Methods to produce chimeric adeno-associated virus/bocavirus parvovirus |
| CA3198936A1 (en) * | 2016-03-07 | 2017-09-14 | University Of Iowa Research Foundation | Aav-mediated expression using a synthetic promoter and enhancer |
| CA3040179A1 (en) * | 2016-10-19 | 2018-04-26 | Adverum Biotechnologies, Inc. | Modified aav capsids and uses thereof |
| CN106928336B (zh) * | 2017-01-20 | 2019-09-24 | 首都医科大学附属北京儿童医院 | 囊性纤维化患者的cftr基因突变形式及其应用 |
| AU2018227483A1 (en) * | 2017-02-28 | 2019-09-12 | Adverum Biotechnologies, Inc. | Modified AAV capsids and uses thereof |
| CN110770346B (zh) * | 2017-03-15 | 2024-01-12 | 北卡罗来纳-查佩尔山大学 | 多倍体腺相关病毒载体及其制备和使用方法 |
| US20220241436A1 (en) * | 2019-04-15 | 2022-08-04 | University Of Iowa Research Foundation | Compositions and methods for treatment of cystic fibrosis |
-
2020
- 2020-04-15 EP EP20727413.5A patent/EP3955970A1/en not_active Withdrawn
- 2020-04-15 PH PH1/2021/552609A patent/PH12021552609A1/en unknown
- 2020-04-15 AU AU2020257182A patent/AU2020257182A1/en not_active Abandoned
- 2020-04-15 CA CA3137078A patent/CA3137078A1/en active Pending
- 2020-04-15 KR KR1020217037211A patent/KR20220047538A/ko not_active Ceased
- 2020-04-15 MX MX2021012682A patent/MX2021012682A/es unknown
- 2020-04-15 CN CN202080043579.3A patent/CN114340683A/zh active Pending
- 2020-04-15 BR BR112021020706A patent/BR112021020706A2/pt unknown
- 2020-04-15 SG SG11202111353QA patent/SG11202111353QA/en unknown
- 2020-04-15 US US17/603,840 patent/US20220195461A1/en not_active Abandoned
- 2020-04-15 JP JP2021561893A patent/JP2022529470A/ja active Pending
- 2020-04-15 WO PCT/US2020/028269 patent/WO2020214672A1/en not_active Ceased
-
2021
- 2021-10-14 IL IL287262A patent/IL287262A/en unknown
-
2023
- 2023-07-21 JP JP2023119196A patent/JP2023126658A/ja active Pending
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