JP2022554300A5 - - Google Patents

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Publication number
JP2022554300A5
JP2022554300A5 JP2022525387A JP2022525387A JP2022554300A5 JP 2022554300 A5 JP2022554300 A5 JP 2022554300A5 JP 2022525387 A JP2022525387 A JP 2022525387A JP 2022525387 A JP2022525387 A JP 2022525387A JP 2022554300 A5 JP2022554300 A5 JP 2022554300A5
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JP
Japan
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sequence
seq
vector system
otof
dual vector
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JP2022525387A
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Japanese (ja)
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JP7665609B2 (ja
JP2022554300A (ja
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Priority claimed from PCT/US2020/058265 external-priority patent/WO2021087296A1/en
Publication of JP2022554300A publication Critical patent/JP2022554300A/ja
Publication of JP2022554300A5 publication Critical patent/JP2022554300A5/ja
Priority to JP2025064211A priority Critical patent/JP2025106464A/ja
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Publication of JP7665609B2 publication Critical patent/JP7665609B2/ja
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JP2022525387A 2019-10-30 2020-10-30 オトフェリン二重ベクター系及びそれを含む感音難聴を治療するための組成物 Active JP7665609B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025064211A JP2025106464A (ja) 2019-10-30 2025-04-09 オトフェリン二重ベクター系を使用して、感音難聴を治療するための組成物及び方法

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US201962928290P 2019-10-30 2019-10-30
US62/928,290 2019-10-30
US202062965776P 2020-01-24 2020-01-24
US62/965,776 2020-01-24
US202062971504P 2020-02-07 2020-02-07
US62/971,504 2020-02-07
US202063023058P 2020-05-11 2020-05-11
US63/023,058 2020-05-11
PCT/US2020/058265 WO2021087296A1 (en) 2019-10-30 2020-10-30 Compositions and methods for treating sensorineural hearing loss using otoferlin dual vector systems

Related Child Applications (1)

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JP2025064211A Division JP2025106464A (ja) 2019-10-30 2025-04-09 オトフェリン二重ベクター系を使用して、感音難聴を治療するための組成物及び方法

Publications (3)

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JP2022554300A JP2022554300A (ja) 2022-12-28
JP2022554300A5 true JP2022554300A5 (enExample) 2023-11-02
JP7665609B2 JP7665609B2 (ja) 2025-04-21

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JP2022525387A Active JP7665609B2 (ja) 2019-10-30 2020-10-30 オトフェリン二重ベクター系及びそれを含む感音難聴を治療するための組成物
JP2025064211A Pending JP2025106464A (ja) 2019-10-30 2025-04-09 オトフェリン二重ベクター系を使用して、感音難聴を治療するための組成物及び方法

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JP2025064211A Pending JP2025106464A (ja) 2019-10-30 2025-04-09 オトフェリン二重ベクター系を使用して、感音難聴を治療するための組成物及び方法

Country Status (11)

Country Link
US (1) US12589168B2 (enExample)
EP (1) EP4051698A4 (enExample)
JP (2) JP7665609B2 (enExample)
KR (1) KR20220130093A (enExample)
AU (1) AU2020375947A1 (enExample)
BR (1) BR112022008214A2 (enExample)
CA (1) CA3159549A1 (enExample)
IL (1) IL292620A (enExample)
MX (1) MX2022005236A (enExample)
TW (1) TWI896570B (enExample)
WO (1) WO2021087296A1 (enExample)

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IL322655A (en) 2023-02-17 2025-10-01 Decibel Therapeutics Inc Method and compositions for administering a dual autopralin vector system

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